Amyloidosis, synucleinopathy, and prion encephalopathy in a neuropathic lysosomal storage disease: the CNS-biomarker potential of peripheral blood.

Amyloidosis, synucleinopathy, and prion encephalopathy in a neuropathic lysosomal storage disease: the CNS-biomarker potential of peripheral blood.

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http://www.wikidata.org/entity/Q35053456
Lysosomal storage disease: gene therapy on both sides of the blood-brain barrier.A GLP-Compliant Toxicology and Biodistribution Study: Systemic Delivery of an rAAV9 Vector for the Treatment of Mucopolysaccharidosis IIIB.Serum global metabolomics profiling reveals profound metabolic impairments in patients with MPS IIIA and MPS IIIB.Adeno-Associated Virus-Based Gene Therapy for CNS Diseases.Near-Complete Correction of Profound Metabolomic Impairments Corresponding to Functional Benefit in MPS IIIB Mice after IV rAAV9-hNAGLU Gene Delivery.Broad functional correction of molecular impairments by systemic delivery of scAAVrh74-hSGSH gene delivery in MPS IIIA mice.Biochemical, histological and functional correction of mucopolysaccharidosis type IIIB by intra-cerebrospinal fluid gene therapy.Blood genome-wide transcriptional profiles reflect broad molecular impairments and strong blood-brain links in Alzheimer's disease.Evaluation of enzyme dose and dose-frequency in ameliorating substrate accumulation in MPS IIIA Huntaway dog brain.
P2860

Amyloidosis, synucleinopathy, and prion encephalopathy in a neuropathic lysosomal storage disease: the CNS-biomarker potential of peripheral blood.

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http://www.wikidata.org/entity/Q35053456
description
2013 nî lūn-bûn
@nan
2013 թուականի Նոյեմբերին հրատարակուած գիտական յօդուած
@hyw
2013 թվականի նոյեմբերին հրատարակված գիտական հոդված
@hy
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
name
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@ast
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@en
type
label
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@ast
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@en
prefLabel
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@ast
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@en
P1433
P1476
P2093
P2860
P304
P31
P356
P407
P433
P478
P577
P5875
P698
P921
P932
P356
P1433
P1476
Amyloidosis, synucleinopathy, ...... potential of peripheral blood.
@en
P2093
P2860
P304
P31
P356
10.1371/JOURNAL.PONE.0080142
P407
P433
P478
P577
P5875
P698
P921
P932