Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy
about
New therapeutic approaches for Krabbe disease: The potential of pharmacological chaperonesLysosomal Re-acidification Prevents Lysosphingolipid-Induced Lysosomal Impairment and Cellular ToxicityCombined gene/cell therapies provide long-term and pervasive rescue of multiple pathological symptoms in a murine model of globoid cell leukodystrophy.Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophyOn the role of natural killer cells in neurodegenerative diseasesExperimental therapies in the murine model of globoid cell leukodystrophy.Gene therapy for lysosomal storage disorders: a good start.Mechanism-based combination treatment dramatically increases therapeutic efficacy in murine globoid cell leukodystrophyAzasugar inhibitors as pharmacological chaperones for Krabbe diseaseNeuroinflammatory paradigms in lysosomal storage diseases.Long-term Improvements in Lifespan and Pathology in CNS and PNS After BMT Plus One Intravenous Injection of AAVrh10-GALC in Twitcher MiceMultipotent stromal cells alleviate inflammation, neuropathology, and symptoms associated with globoid cell leukodystrophy in the twitcher mouse.Cellular transplant therapies for globoid cell leukodystrophy: Preclinical and clinical observationsCombination Therapies for Lysosomal Storage Diseases: A Complex Answer to a Simple Problem.Krabbe disease: One Hundred years from the bedside to the bench to the bedside.Treatment for Krabbe's disease: Finding the combination.Chaperones as potential therapeutics for Krabbe disease.Perspective on innovative therapies for globoid cell leukodystrophy.Immunological considerations for treating globoid cell leukodystrophy.A HILIC-MS/MS method for simultaneous quantification of the lysosomal disease markers galactosylsphingosine and glucosylsphingosine in mouse serum
P2860
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P2860
Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy
description
2012 nî lūn-bûn
@nan
2012年の論文
@ja
2012年論文
@yue
2012年論文
@zh-hant
2012年論文
@zh-hk
2012年論文
@zh-mo
2012年論文
@zh-tw
2012年论文
@wuu
2012年论文
@zh
2012年论文
@zh-cn
name
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@ast
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@en
type
label
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@ast
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@en
prefLabel
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@ast
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@en
P2093
P2860
P1476
Bone marrow transplantation in ...... of globoid cell leukodystrophy
@en
P2093
Adarsh S Reddy
Daniel S Ory
Elizabeth Y Qin
Jacqueline A Hawkins-Salsbury
Nuri B Farber
Xuntian Jiang
P2860
P304
P356
10.1016/J.YMGME.2012.05.021
P50
P577
2012-06-01T00:00:00Z