Adeno-associated virus-based gene therapy for inherited disorders.
about
Adeno-associated virus for cystic fibrosis gene therapyEnhanced transduction of colonic cell lines in vitro and the inflamed colon in mice by viral vectors, derived from adeno-associated virus serotype 2, using virus-microbead conjugates bearing lectin.Application of a haematopoetic progenitor cell-targeted adeno-associated viral (AAV) vector established by selection of an AAV random peptide library on a leukaemia cell line.RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy.Cardiac gene therapyDown-regulation of expression of rat pyruvate dehydrogenase E1alpha gene by self-complementary adeno-associated virus-mediated small interfering RNA delivery.AAV-based neonatal gene therapy for hemophilia A: long-term correction and avoidance of immune responses in miceDevelopment of lentiviral vectors with regulated respiratory epithelial expression in vivoThe promise of gene therapy for the treatment of alpha-1 antitrypsin deficiency.Disorders of protein misfolding: alpha-1-antitrypsin deficiency as prototype.Towards a rAAV-based gene therapy for ADA-SCID: from ADA deficiency to current and future treatment strategies.Cardiac gene therapy with SERCA2a: from bench to bedsideCardiac gene therapy: from concept to reality.Lentiviral vectors and cystic fibrosis gene therapyRecombinant AAV serotype and capsid mutant comparison for pulmonary gene transfer of alpha-1-antitrypsin using invasive and noninvasive deliveryEfficient gene transfer with pseudotyped recombinant adeno-associated viral vectors into human chronic myelogenous leukemia cells.Thermal Stability as a Determinant of AAV Serotype Identity.Prenatal gene therapy for the early treatment of genetic disorders
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P2860
Adeno-associated virus-based gene therapy for inherited disorders.
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年学术文章
@wuu
2005年学术文章
@zh-cn
2005年学术文章
@zh-hans
2005年学术文章
@zh-my
2005年学术文章
@zh-sg
2005年學術文章
@yue
2005年學術文章
@zh
2005年學術文章
@zh-hant
name
Adeno-associated virus-based gene therapy for inherited disorders.
@ast
Adeno-associated virus-based gene therapy for inherited disorders.
@en
type
label
Adeno-associated virus-based gene therapy for inherited disorders.
@ast
Adeno-associated virus-based gene therapy for inherited disorders.
@en
prefLabel
Adeno-associated virus-based gene therapy for inherited disorders.
@ast
Adeno-associated virus-based gene therapy for inherited disorders.
@en
P2860
P1433
P1476
Adeno-associated virus-based gene therapy for inherited disorders.
@en
P2093
Terence R Flotte
P2860
P304
P356
10.1203/01.PDR.0000189226.03684.FE
P407
P577
2005-12-01T00:00:00Z
P5875
P6179
1021304970