Elusive sources of variability of dystrophin rescue by exon skipping
about
Clinical utility of serum biomarkers in Duchenne muscular dystrophyDigital Droplet PCR for the Absolute Quantification of Exon Skipping Induced by Antisense Oligonucleotides in (Pre-)Clinical Development for Duchenne Muscular Dystrophy.In vivo gene editing in dystrophic mouse muscle and muscle stem cells.Mitochondria mediate cell membrane repair and contribute to Duchenne muscular dystrophy.Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle.Functional improvement of dystrophic muscle by repression of utrophin: let-7c interaction.An amphipathic trans-acting phosphorothioate RNA element delivers an uncharged phosphorodiamidate morpholino sequence in mdx mouse myotubes.
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P2860
Elusive sources of variability of dystrophin rescue by exon skipping
description
2015 nî lūn-bûn
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2015年の論文
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2015年学术文章
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2015年学术文章
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name
Elusive sources of variability of dystrophin rescue by exon skipping
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Elusive sources of variability of dystrophin rescue by exon skipping
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type
label
Elusive sources of variability of dystrophin rescue by exon skipping
@ast
Elusive sources of variability of dystrophin rescue by exon skipping
@en
prefLabel
Elusive sources of variability of dystrophin rescue by exon skipping
@ast
Elusive sources of variability of dystrophin rescue by exon skipping
@en
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P2860
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Elusive sources of variability of dystrophin rescue by exon skipping
@en
P2093
Aiping Zhang
Conner Shaughnessy
Eric P Hoffman
Heather Gordish-Dressman
Jessica F Boehler
John van den Anker
Kristy J Brown
Margaret Benny Klimek
Qi Long Lu
Sree Rayavarapu
P2860
P2888
P356
10.1186/S13395-015-0070-6
P50
P577
2015-12-01T00:00:00Z
P5875
P6179
1014345223