Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.
about
Animal models of β-hemoglobinopathies: utility and limitationsRetroviral vectors and transposons for stable gene therapy: advances, current challenges and perspectivesGene Therapy 2017: Progress and Future Directions.Genome editing using CRISPR-Cas9 to create the HPFH genotype in HSPCs: An approach for treating sickle cell disease and β-thalassemiaLineage-specific BCL11A knockdown circumvents toxicities and reverses sickle phenotype.Evidence for the in vivo safety of insulated foamy viral vectorsCD34+ cells from dental pulp stem cells with a ZFN-mediated and homology-driven repair-mediated locus-specific knock-in of an artificial β-globin gene.Cell and Gene Therapy for the Beta-Thalassemias: Advances and Prospects.Pediatric sickle cell disease: past successes and future challenges.Current status of ex vivo gene therapy for hematological disorders: a review of clinical trials in Japan around the world.Emerging cellular and gene therapies for congenital anemias.β-Thalassemia.Cure for thalassemia major - from allogeneic hematopoietic stem cell transplantation to gene therapy.Gene Therapy for β-Hemoglobinopathies.Investigational drugs in phase I and phase II clinical trials for thalassemia.Molecular basis of β thalassemia and potential therapeutic targets.Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia.Recent progress in understanding and manipulating haemoglobin switching for the haemoglobinopathies.Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies.Manufacture of Third-Generation Lentivirus for Preclinical Use, with Process Development Considerations for Translation to Good Manufacturing Practice.The Potential of Nanotechnology in Medically Assisted Reproduction.Emerging Therapies.Developing new pharmacotherapeutic approaches to treating sickle-cell disease.MiRNA-16 inhibited oral squamous carcinoma tumor growth in vitro and in vivo via suppressing Wnt/β-catenin signaling pathwayDisruption of the BCL11A Erythroid Enhancer Reactivates Fetal Hemoglobin in Erythroid Cells of Patients with β-Thalassemia MajorGene Therapy for Hemoglobinopathies
P2860
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P2860
Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@ast
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@en
type
label
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@ast
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@en
prefLabel
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@ast
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@en
P2093
P2860
P50
P356
P1433
P1476
Gene Therapy of the β-Hemoglob ...... of the β(A(T87Q))-Globin Gene.
@en
P2093
Anne-Virginie Eggimann
Jean-Antoine Ribeil
Olivier Negre
Philippe Bourget
Salima Hacein-Bey
Suradej Hongeng
Yves Beuzard
P2860
P304
P356
10.1089/HUM.2016.007
P577
2016-02-01T00:00:00Z