A phenotypic compound screening assay for lysosomal storage diseases.
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Flow Cytometry: Impact on Early Drug DiscoveryNeural stem cells for disease modeling of Wolman disease and evaluation of therapeutics.Analytical Characterization of Methyl-β-Cyclodextrin for Pharmacological Activity to Reduce Lysosomal Cholesterol Accumulation in Niemann-Pick Disease Type C1 Cells.Rescue of an in vitro neuron phenotype identified in Niemann-Pick disease, type C1 induced pluripotent stem cell-derived neurons by modulating the WNT pathway and calcium signalingToward reducing immunogenicity of enzyme replacement therapy: altering the specificity of human β-glucuronidase to compensate for α-iduronidase deficiency.Niemann-Pick Disease Type C: Induced Pluripotent Stem Cell-Derived Neuronal Cells for Modeling Neural Disease and Evaluating Drug Efficacy.Lysosomal adaptation: How cells respond to lysosomotropic compounds.TMBIM6 (transmembrane BAX inhibitor motif containing 6) enhances autophagy and reduces renal dysfunction in a cyclosporine A-induced nephrotoxicity modelOne-Step Seeding of Neural Stem Cells with Vitronectin-Supplemented Medium for High-Throughput Screening Assays.Patient fibroblasts-derived induced neurons demonstrate autonomous neuronal defects in adult-onset Krabbe disease.Targeting Wolman Disease and Cholesteryl Ester Storage Disease: Disease Pathogenesis and Therapeutic Development.Contribution of membrane trafficking perturbation to retinal toxicity.High-content screen for modifiers of Niemann-Pick Type C disease in patient cells.Emetine inhibits Zika and Ebola virus infections through two molecular mechanisms: inhibiting viral replication and decreasing viral entry.Glucosylceramide synthase inhibition with lucerastat lowers globotriaosylceramide and lysosome staining in cultured fibroblasts from Fabry patients with different mutation types
P2860
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P2860
A phenotypic compound screening assay for lysosomal storage diseases.
description
2013 nî lūn-bûn
@nan
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
2013年论文
@zh
2013年论文
@zh-cn
name
A phenotypic compound screening assay for lysosomal storage diseases.
@ast
A phenotypic compound screening assay for lysosomal storage diseases.
@en
type
label
A phenotypic compound screening assay for lysosomal storage diseases.
@ast
A phenotypic compound screening assay for lysosomal storage diseases.
@en
prefLabel
A phenotypic compound screening assay for lysosomal storage diseases.
@ast
A phenotypic compound screening assay for lysosomal storage diseases.
@en
P2093
P2860
P356
P1476
A phenotypic compound screening assay for lysosomal storage diseases.
@en
P2093
John C McKew
Manju Swaroop
Seameen J Dehdashti
P2860
P304
P356
10.1177/1087057113501197
P50
P577
2013-08-27T00:00:00Z