Liver-directed adeno-associated virus serotype 8 gene transfer rescues a lethal murine model of citrullinemia type 1. - Wikidata - awgldk - TriplyDB

Liver-directed adeno-associated virus serotype 8 gene transfer rescues a lethal murine model of citrullinemia type 1.

Liver-directed adeno-associated virus serotype 8 gene transfer rescues a lethal murine model of citrullinemia type 1.

http://www.wikidata.org/entity/Q37374275

about

Liver-targeted gene therapy: Approaches and challenges Impaired T cell function in argininosuccinate synthetase deficiency Gene editing technology as an approach to the treatment of liver diseases.Mutations in the Human Argininosuccinate Synthetase (ASS1) Gene, Impact on Patients, Common Changes, and Structural Considerations.Efficient Gene Delivery and Expression in Pancreas and Pancreatic Tumors by Capsid-Optimized AAV8 Vectors.l-Citrulline Metabolism in Mice Augments CD4+ T Cell Proliferation and Cytokine Production In Vitro, and Accumulation in the Mycobacteria-Infected Lung.Argininosuccinic aciduria fosters neuronal nitrosative stress reversed by Asl gene transfer

P2860

Q28085748-75F4017C-694E-4958-BF5F-E4A7FA927907 Q35005894-1DA882BC-8025-4AC6-9878-05B5E6E73BFC Q38749884-1F3CDF61-6726-4612-8A75-5F7DBFDA8842 Q39006194-6A969ADE-6E3D-4DDA-B0CF-BF61727891E6 Q40363171-2D211857-3E95-46F8-B650-D00A91A0DAE0 Q47107446-E5481695-EB4E-45BF-885D-9E7082BF039B Q58695537-5F3F0A93-B5DC-413B-AF0F-AF396827F1CC

P2860

Liver-directed adeno-associated virus serotype 8 gene transfer rescues a lethal murine model of citrullinemia type 1.

http://www.wikidata.org/entity/Q37374275

description

article científic

@ca

article scientifique

@fr

articolo scientifico

@it

artigo científico

@pt

bilimsel makale

@tr

scientific article published on 17 October 2013

@en

vedecký článok

@sk

vetenskaplig artikel

@sv

videnskabelig artikel

@da

vědecký článek

@cs

name

Liver-directed adeno-associate ...... model of citrullinemia type 1.

@en

Liver-directed adeno-associate ...... model of citrullinemia type 1.

@nl

type

label

Liver-directed adeno-associate ...... model of citrullinemia type 1.

@en

Liver-directed adeno-associate ...... model of citrullinemia type 1.

@nl

prefLabel

Liver-directed adeno-associate ...... model of citrullinemia type 1.

@en

Liver-directed adeno-associate ...... model of citrullinemia type 1.

@nl

P1433

Q37374275-A3F4DBC7-B894-4A4C-973D-A6B93BB777F7

P1476

Q37374275-71AD598C-DB93-4C55-9773-174A6A965D1E

P2093

Q37374275-3144A341-5DBD-48C4-8A6F-9299CED2729B

Q37374275-3D4DAF50-3ADE-4DE5-8350-D97F79696F6A

Q37374275-5F9F086F-E2A6-422B-9315-67C88937E62A

Q37374275-8B306B14-0DCB-42F5-B61A-57776008ED5E

Q37374275-91C877D3-F0F8-460A-9D8E-9172E84FDB57

Q37374275-A0B76308-BC99-4FE9-9E2C-CD64EEAF1FE7

P2860

Q37374275-0613D19A-782F-43E4-B3B6-4AA4DFF28F77

Q37374275-193B6701-02D7-44D4-9759-C5430A517C6E

Q37374275-490DBA44-F692-44AF-BF13-0B7F660A99C3

Q37374275-69EBA8B5-72E4-40A5-9AE6-594D2C1743BB

Q37374275-772AAF49-033E-463A-9CB6-E3C654224E74

Q37374275-7837B114-98FE-444C-99E8-69284D6174D9

Q37374275-880A4F83-4B99-46BF-B773-D3BF9A9C6D70

Q37374275-8BC7E64A-56C9-4FDB-AD53-892D7A883761

Q37374275-9DA9483A-C98B-4D2E-9E3C-2A0543FF275F

Q37374275-AEFD87CA-C4C2-41DB-AFA8-6EBDD243DBFF

P2888

Q37374275-334985BB-C447-48F1-98CC-DA2C295BBBD9

P304

Q37374275-3027C4CC-B0BD-4DE7-9C70-7CA5ABB550C7

P31

Q37374275-43D4E1F5-8264-4CB2-992F-389DCCE15693

P356

Q37374275-14AACC8B-32E7-4D48-B907-1B465D296C21

P433

Q37374275-889C1FF6-D087-48C4-887D-6BE88D76BE55

P478

Q37374275-2F82A6C8-E27D-4FA1-AC9E-C3D5EDC96FB6

P50

Q37374275-04FBC6FE-018B-4D03-93BB-FF91DEC39D78

P577

Q37374275-00728708-1FA0-4E1F-944E-F00EF8F14962

P5875

Q37374275-B09FDF79-4628-4D9D-956B-5296A5B2553D

P698

Q37374275-AB9731AF-9AAE-4E6D-A4C8-ECF2E8ED9938

P932

Q37374275-620EE1FB-0C39-4681-8465-6C23CFE65356

P356

P1433

P1476

Liver-directed adeno-associate ...... model of citrullinemia type 1

@en

P2093

C P Venditti

http://www.w3.org/2001/XMLSchema#string

K Cusmano-Ozog

http://www.w3.org/2001/XMLSchema#string

P J McGuire

http://www.w3.org/2001/XMLSchema#string

Q Sun

http://www.w3.org/2001/XMLSchema#string

T N Tarasenko

http://www.w3.org/2001/XMLSchema#string

V R Sutton

http://www.w3.org/2001/XMLSchema#string

P2860

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)

AAV2/8-mediated correction of OTC deficiency is robust in adult but not neonatal Spf(ash) mice.

Two hypomorphic alleles of mouse Ass1 as a new animal model of citrullinemia type I and other hyperammonemic syndromes.

Current role of liver transplantation for the treatment of urea cycle disorders: a review of the worldwide English literature and 13 cases at Kyoto University.

Adeno-associated virus serotype 8 gene transfer rescues a neonatal lethal murine model of propionic acidemia.

The role of liver transplantation in urea cycle disorders.

Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome.

Renal arginine metabolism.

Helper-dependent adenoviral vectors for gene therapy.

P2888

P304

1188-1191

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.1038/GT.2013.53

http://www.w3.org/2001/XMLSchema#string

P433

12

http://www.w3.org/2001/XMLSchema#string

P478

20

http://www.w3.org/2001/XMLSchema#string

P50

P577

2013-10-17T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P5875

257888849

http://www.w3.org/2001/XMLSchema#string

P698

24131980

http://www.w3.org/2001/XMLSchema#string

P932

3855546

http://www.w3.org/2001/XMLSchema#string