Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)
about
Vector design influences hepatic genotoxicity after adeno-associated virus gene therapy.Neutralizing Antibodies Against Adeno-Associated Viral Capsids in Patients with mut Methylmalonic Acidemia.Vitamin B(12) metabolism during pregnancy and in embryonic mouse models.Liver-directed adeno-associated virus serotype 8 gene transfer rescues a lethal murine model of citrullinemia type 1.Current concepts in organic acidurias: understanding intra- and extracerebral disease manifestation.
P2860
Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)
description
2012 nî lūn-bûn
@nan
2012 թուականի Նոյեմբերին հրատարակուած գիտական յօդուած
@hyw
2012 թվականի նոյեմբերին հրատարակված գիտական հոդված
@hy
2012年の論文
@ja
2012年論文
@yue
2012年論文
@zh-hant
2012年論文
@zh-hk
2012年論文
@zh-mo
2012年論文
@zh-tw
2012年论文
@wuu
name
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@ast
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@en
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@nl
type
label
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@ast
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@en
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@nl
prefLabel
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@ast
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@en
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@nl
P2860
P1476
Pre-clinical efficacy and dosi ...... f methylmalonic acidemia (MMA)
@en
P2093
Charles P Venditti
Randy J Chandler
P2860
P356
10.1016/J.YMGME.2012.09.019
P407
P577
2012-11-01T00:00:00Z