Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
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Myotonic disorders: A review articleTwisting right to left: A…A mismatch in a CAG trinucleotide repeat overexpansion provokes left-handed Z-DNA conformationCell membrane integrity in myotonic dystrophy type 1: implications for therapyPremutation CGG-repeat expansion of the Fmr1 gene impairs mouse neocortical development.Molecular, physiological, and motor performance defects in DMSXL mice carrying >1,000 CTG repeats from the human DM1 locus.Developing bivalent ligands to target CUG triplet repeats, the causative agent of myotonic dystrophy type 1.Aging--RNA in development and disease.On the Applicability of Elastic Network Models for the Study of RNA CUG Trinucleotide Repeat Overexpansion.Design and analysis of effects of triplet repeat oligonucleotides in cell models for myotonic dystrophyPerspectives on gene therapy in myotonic dystrophy type 1.Targeting RNA to treat neuromuscular disease.Silencing human genetic diseases with oligonucleotide-based therapies.Structure and Dynamics of RNA Repeat Expansions That Cause Huntington's Disease and Myotonic Dystrophy Type 1.A Ligand That Targets CUG Trinucleotide Repeats.
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P2860
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 20 April 2010
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
@en
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
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type
label
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
@en
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
@nl
prefLabel
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
@en
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
@nl
P2093
P2860
P356
P1476
Molecular therapy in myotonic dystrophy: focus on RNA gain-of-function.
@en
P2093
Baziel G M van Engelen
Bé Wieringa
Derick G Wansink
Susan A M Mulders
P2860
P356
10.1093/HMG/DDQ161
P577
2010-04-20T00:00:00Z