about
Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patientsβ-thalassemia: a model for elucidating the dynamic regulation of ineffective erythropoiesis and iron metabolism.Gene therapy for hemoglobinopathies: progress and challenges.Anemia, ineffective erythropoiesis, and hepcidin: interacting factors in abnormal iron metabolism leading to iron overload in β-thalassemia.A preclinical approach for gene therapy of beta-thalassemia.A combined approach for β-thalassemia based on gene therapy-mediated adult hemoglobin (HbA) production and fetal hemoglobin (HbF) induction.Ground state naïve pluripotent stem cells and CRISPR/Cas9 gene correction for β-thalassemia.Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia.Orphan Drugs and Potential Novel Approaches for Therapies of β-Thalassemia: Current Status and Future Expectations
P2860
Q28730903-0115C24A-E4BB-4557-B600-10C9FF979373Q35485724-1D62123A-275F-4EF7-9DB0-DE4B71F8FF28Q37027448-057677D6-050D-437A-9EAF-0104BCF76254Q37809337-B98A9D91-146C-40E4-8CB2-2442611054D3Q41889977-2656C90B-334A-4E6D-A12F-5CC579214583Q42224585-33E1E8B0-5BF7-486C-A201-40ACBA7E77A6Q42370396-99611BE6-CF36-4F55-A115-83FEBBD80596Q45874313-874830F6-66C4-40F9-BA08-B9CD7805BAE3Q54585888-BD70A791-0EFB-4D12-94E9-C89D6458C138
P2860
description
2009 nî lūn-bûn
@nan
2009年の論文
@ja
2009年学术文章
@wuu
2009年学术文章
@zh-cn
2009年学术文章
@zh-hans
2009年学术文章
@zh-my
2009年学术文章
@zh-sg
2009年學術文章
@yue
2009年學術文章
@zh
2009年學術文章
@zh-hant
name
Gene therapy in thalassemia and hemoglobinopathies.
@en
Gene therapy in thalassemia and hemoglobinopathies.
@nl
type
label
Gene therapy in thalassemia and hemoglobinopathies.
@en
Gene therapy in thalassemia and hemoglobinopathies.
@nl
prefLabel
Gene therapy in thalassemia and hemoglobinopathies.
@en
Gene therapy in thalassemia and hemoglobinopathies.
@nl
P2860
P356
P1476
Gene therapy in thalassemia and hemoglobinopathies
@en
P2093
Roberto Gambari
P2860
P304
P356
10.4084/MJHID.2009.008
P577
2009-11-13T00:00:00Z