Therapeutic approaches for spinal muscular atrophy (SMA).
about
Treatment Advances in Spinal Muscular Atrophy.Motor Neuron Gene Therapy: Lessons from Spinal Muscular Atrophy for Amyotrophic Lateral Sclerosis.Overview of Current Drugs and Molecules in Development for Spinal Muscular Atrophy Therapy.Effects of Arm Cycling Exercise in Spinal Muscular Atrophy Type II Patients: A Pilot Study.Chemistry, mechanism and clinical status of antisense oligonucleotides and duplex RNAs.Exon Specific U1 snRNAs improve ELP1 exon 20 definition and rescue ELP1 protein expression in a Familial Dysautonomia mouse model.Neurochemical abnormalities in premanifest and early spinocerebellar ataxias.Spinal muscular atrophy type I and the dual role of viruses: An interview with Professor Basil T. Darras, Professor of Neurology (Pediatrics) at Harvard Medical School.Adeno-associated Virus Genome Population Sequencing Achieves Full Vector Genome Resolution and Reveals Human-Vector Chimeras.Alternative mRNA Splicing in the Pathogenesis of Obesity.Position Statement: Sharing of Clinical Research Data in Spinal Muscular Atrophy to Accelerate Research and Improve Outcomes for Patients.Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening.Autism spectrum disorder: prospects for treatment using gene therapy.Ambulatory function in spinal muscular atrophy: Age-related patterns of progression.Evaluation of potential effects of Plastin 3 overexpression and low-dose SMN-antisense oligonucleotides on putative biomarkers in spinal muscular atrophy mice
P2860
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P2860
Therapeutic approaches for spinal muscular atrophy (SMA).
description
2017 nî lūn-bûn
@nan
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
2017年论文
@zh
2017年论文
@zh-cn
name
Therapeutic approaches for spinal muscular atrophy (SMA).
@en
Therapeutic approaches for spinal muscular atrophy
@nl
type
label
Therapeutic approaches for spinal muscular atrophy (SMA).
@en
Therapeutic approaches for spinal muscular atrophy
@nl
prefLabel
Therapeutic approaches for spinal muscular atrophy (SMA).
@en
Therapeutic approaches for spinal muscular atrophy
@nl
P2093
P2860
P356
P1433
P1476
Therapeutic approaches for spinal muscular atrophy (SMA).
@en
P2093
P2860
P2888
P304
P356
10.1038/GT.2017.45
P577
2017-05-31T00:00:00Z
P6179
1085735135