Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency.
about
Advances of gene therapy for primary immunodeficienciesRecent advances in treatment of severe primary immunodeficienciesUse of V(D)J recombination excision circles to identify T- and B-cell defects and to monitor the treatment in primary and acquired immunodeficienciesAutoimmune dysregulation and purine metabolism in adenosine deaminase deficiency.Concise review: lessons learned from clinical trials of gene therapy in monogenic immunodeficiency diseases.Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products.Comparison of outcomes of hematopoietic stem cell transplantation without chemotherapy conditioning by using matched sibling and unrelated donors for treatment of severe combined immunodeficiency.Gene transfer into hematopoietic stem cells as treatment for primary immunodeficiency diseases.Gene therapy for inherited immunodeficiency.Hematopoietic stem cell transplantation for primary immunodeficiencies.Clinical applications of gene therapy for primary immunodeficiencies.What has happened in the last 50 years in immunology.History and current status of newborn screening for severe combined immunodeficiency.B-cell development and functions and therapeutic options in adenosine deaminase-deficient patients.Intrathymic progenitor cell transplantation across histocompatibility barriers results in the persistence of early thymic progenitors and T-cell differentiation.Cost-Effectiveness/Cost-Benefit Analysis of Newborn Screening for Severe Combined Immune Deficiency in Washington StateLong-term outcome of non-ablative booster BMT in patients with SCIDUpdate on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency.Gene therapy for primary immune deficiencies: a Canadian perspective.Haematopoietic stem cell transplantation for SCID patients: where do we stand?Concise review: hematopoietic stem cell transplantation: targeting the thymus.Unresolved issues in hematopoietic stem cell transplantation for severe combined immunodeficiency: need for safer conditioning and reduced late effects.Lentiviral vectors for the treatment of primary immunodeficiencies.Moonlighting adenosine deaminase: a target protein for drug development.Inborn errors of metabolism underlying primary immunodeficiencies.Primary immunodeficiencies: a decade of shifting paradigms, the current status and the emergence of cutting-edge therapies and diagnostics.Severe combined immunodeficiency: recent developments and guidance on clinical management.Gene therapy for primary immunodeficiencies.Current Knowledge and Priorities for Future Research in Late Effects after Hematopoietic Stem Cell Transplantation (HCT) for Severe Combined Immunodeficiency Patients: A Consensus Statement from the Second Pediatric Blood and Marrow Transplant ConsoErythrocyte-mediated delivery of recombinant enzymes.Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.Treatment of infants identified as having severe combined immunodeficiency by means of newborn screening.Periodontal and other oral manifestations of immunodeficiency diseases.How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID).Evolving Gene Therapy in Primary Immunodeficiency.Primary immunodeficiencies worldwide: an updated overview from the Jeffrey Modell Centers Global Network.Long-Term Outcome of Adenosine Deaminase-Deficient Patients-a Single-Center Experience.Infusion of Sibling Marrow in a Patient with Purine Nucleoside Phosphorylase Deficiency Leads to Split Mixed Donor Chimerism and Normal Immunity.Diagnosis, Treatment and Long-Term Follow Up of Patients with ADA Deficiency: a Single-Center Experience.Longitudinal Evaluation of Immune Reconstitution and B-cell Function After Hematopoietic Cell Transplantation for Primary Immunodeficiency.
P2860
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P2860
Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency.
description
2012 nî lūn-bûn
@nan
2012年の論文
@ja
2012年学术文章
@wuu
2012年学术文章
@zh
2012年学术文章
@zh-cn
2012年学术文章
@zh-hans
2012年学术文章
@zh-my
2012年学术文章
@zh-sg
2012年學術文章
@yue
2012年學術文章
@zh-hant
name
Outcome of hematopoietic stem ...... ere combined immunodeficiency.
@en
Outcome of hematopoietic stem ...... ere combined immunodeficiency.
@nl
type
label
Outcome of hematopoietic stem ...... ere combined immunodeficiency.
@en
Outcome of hematopoietic stem ...... ere combined immunodeficiency.
@nl
prefLabel
Outcome of hematopoietic stem ...... ere combined immunodeficiency.
@en
Outcome of hematopoietic stem ...... ere combined immunodeficiency.
@nl
P2093
P50
P1433
P1476
Outcome of hematopoietic stem ...... vere combined immunodeficiency
@en
P2093
Abdulaziz Al Ghonaium
Alain Fischer
Alex Brightwell
Alexandra Filipovich
Amel Hassan
Andrew Gennery
Arnalda Lanfranchi
Chaim M Roifman
Daifulah Al Zahrani
E Graham Davies
P304
3615-24; quiz 3626
P356
10.1182/BLOOD-2011-12-396879
P407
P50
P577
2012-07-12T00:00:00Z