Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome.
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Enzyme replacement therapy with laronidase (Aldurazyme®) for treating mucopolysaccharidosis type IEnzyme replacement therapy with laronidase (Aldurazyme) for treating mucopolysaccharidosis type IEnzyme replacement therapy with laronidase (Aldurazyme®) for treating mucopolysaccharidosis type ITherapies for the bone in mucopolysaccharidosesGrowth patterns and the use of growth hormone in the mucopolysaccharidoses.Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure.Diagnosis and treatment trends in mucopolysaccharidosis I: findings from the MPS I Registry.Short-term growth hormone treatment in children with Hurler syndrome after hematopoietic cell transplantationClinical outcomes following hematopoietic stem cell transplantation for the treatment of mucopolysaccharidosis VICombined Enzyme Replacement Therapy and Hematopoietic Stem Cell Transplantation in Mucopolysacharidosis Type VI.Therapy for the mucopolysaccharidoses.Current and potential therapeutic strategies for mucopolysaccharidoses.Stem Cell Therapy for the Central Nervous System in Lysosomal Storage Diseases.Long term survival and cardiopulmonary outcome in children with Hurler syndrome after haematopoietic stem cell transplantation.alpha-L-iduronidase therapy for mucopolysaccharidosis type I.Substrate Deprivation Therapy to Reduce Glycosaminoglycan Synthesis Improves Aspects of Neurological and Skeletal Pathology in MPS I Mice.Precocious initiation of spermatogenesis in a 19-month-old boy with Hurler syndrome.Minimum requirement of donor cells to reduce the glycolipid storage following bone marrow transplantation in a murine model of Fabry disease.Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome.Pre-transplant risk factors affecting outcome in Hurler syndrome.The Nature of the Pediatric Brain and Its Associated Diseases Precludes Adult Surrogates for Testing Intracranial Stem Cell-Based Transplantation StrategiesShort stature as a presenting symptom of attenuated Mucopolysaccharidosis type I: case report and clinical insights
P2860
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P2860
Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome.
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年学术文章
@wuu
2005年学术文章
@zh-cn
2005年学术文章
@zh-hans
2005年学术文章
@zh-my
2005年学术文章
@zh-sg
2005年學術文章
@yue
2005年學術文章
@zh
2005年學術文章
@zh-hant
name
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@en
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@nl
type
label
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@en
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@nl
prefLabel
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@en
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@nl
P2093
P2860
P1433
P1476
Safety and efficacy of enzyme ...... plantation in Hurler syndrome.
@en
P2093
Annet van Royen-Kerkhof
Barbara K Burton
Charles Peters
Chester B Whitley
Claudia Haase
David Sillence
George E Tiller
Guy A Young
James E Wraith
Jose E Abdenur
P2860
P304
P356
10.1097/01.GIM.0000154299.22120.6A
P407
P577
2005-02-01T00:00:00Z
P6179
1015268581