Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

about

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

Item

http://www.wikidata.org/entity/Q52675066

description

2018 nî lūn-bûn

@nan

2018年の論文

@ja

2018年学术文章

@wuu

2018年学术文章

@zh

2018年学术文章

@zh-cn

2018年学术文章

@zh-hans

2018年学术文章

@zh-my

2018年学术文章

@zh-sg

2018年學術文章

@yue

2018年學術文章

@zh-hant

name

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@en

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@nl

type

Item

label

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@en

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@nl

prefLabel

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@en

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@nl

P1476

Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.

@en

P2093

Barry J Byrne

http://www.w3.org/2001/XMLSchema#string

P2860

Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.

Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brain

Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in children affected by Pompe Disease.

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.

Severe toxicity in nonhuman primates and piglets following high-dose intravenous administration of an AAV vector expressing human SMN.

Severe Toxicity in Nonhuman Primates and Piglets with Systemic High-Dose Administration of Adeno-Associated Virus Serotype 9-Like Vectors: Putting Patients First.

The Neurotropic Properties of AAV-PHP.B Are Limited to C57BL/6J Mice.

Toxicology and Biodistribution: The Clinical Value of Animal Biodistribution Studies.

P304

669-671

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.1016/J.YMTHE.2018.02.009

http://www.w3.org/2001/XMLSchema#string

P433

http://www.w3.org/2001/XMLSchema#string

P478

http://www.w3.org/2001/XMLSchema#string

P577

2018-03-01T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P698

29503193

http://www.w3.org/2001/XMLSchema#string

P921

gene therapy

P932

5911637

http://www.w3.org/2001/XMLSchema#string