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Q52675066-1D05120E-644F-4449-AEF3-5224BAB94D56
Q52675066-1D05120E-644F-4449-AEF3-5224BAB94D56
BestRank
Statement
http://www.wikidata.org/entity/statement/Q52675066-1D05120E-644F-4449-AEF3-5224BAB94D56
Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.
P2860
Q52675066-1D05120E-644F-4449-AEF3-5224BAB94D56
BestRank
Statement
http://www.wikidata.org/entity/statement/Q52675066-1D05120E-644F-4449-AEF3-5224BAB94D56
rank
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Statement
wasDerivedFrom
3c919279fcc998485e9a42c9e1e138c20e1f116f
P2860
Severe toxicity in nonhuman primates and piglets following high-dose intravenous administration of an AAV vector expressing human SMN.