Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Item
http://www.wikidata.org/entity/Q56518421
Short-hairpin RNA against aberrant HBB[IVSI-110(G>A)] mRNA restores β-globin levels in a novel cell model and acts as mono- and combination therapy for β-thalassemia in primary hematopoietic stem cells.Efficient Transduction and Expansion of Ovine Macrophages for Gene Therapy Implementations.Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-ThalassemiaEfficacy of Oral Acetaminophen and Intravenous Chlorpheniramine Maleate versus Placebo to Prevent Red Cell Transfusion Reactions in Children and Adolescent with Thalassemia: A Prospective, Randomized, Double-Blind Controlled TrialFrom scientific discovery to treatments for rare diseases - the view from the National Center for Advancing Translational Sciences - Office of Rare Diseases ResearchGene Therapy for HemoglobinopathiesAn Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype
P2860

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Item
http://www.wikidata.org/entity/Q56518421
description
article
@en
im April 2018 veröffentlichter wissenschaftlicher Artikel
@de
wetenschappelijk artikel
@nl
наукова стаття, опублікована у квітні 2018
@uk
ലേഖനം
@ml
name
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@en
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@nl
type
label
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@en
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@nl
prefLabel
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@en
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@nl
P1433
P1476
P2093
P304
P31
P356
P407
P433
P478
P50
P577
P698
P356
P1433
P1476
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
@en
P2093
P304
P31
P356
P407
P433
P478
P50
P577
P698