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Q28276617-22D0517A-1CE7-4F9F-A0F6-3D8B3B164D91
Q28276617-22D0517A-1CE7-4F9F-A0F6-3D8B3B164D91
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http://www.wikidata.org/entity/statement/Q28276617-22D0517A-1CE7-4F9F-A0F6-3D8B3B164D91
Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)
P2860
Q28276617-22D0517A-1CE7-4F9F-A0F6-3D8B3B164D91
BestRank
Statement
http://www.wikidata.org/entity/statement/Q28276617-22D0517A-1CE7-4F9F-A0F6-3D8B3B164D91
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f9fc5634a446eca425165359d67ea4091dcd1c3f
P2860
Rapid diagnosis of methylmalonic and propionic acidemias: quantitative tandem mass spectrometric analysis of propionylcarnitine in filter-paper blood specimens obtained from newborns.