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Q34085940-80A7E950-E22B-4F19-8048-7E1FC44F15DB
Q34085940-80A7E950-E22B-4F19-8048-7E1FC44F15DB
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http://www.wikidata.org/entity/statement/Q34085940-80A7E950-E22B-4F19-8048-7E1FC44F15DB
Replacement gene therapy with a human RPGRIP1 sequence slows photoreceptor degeneration in a murine model of Leber congenital amaurosis.
P2860
Q34085940-80A7E950-E22B-4F19-8048-7E1FC44F15DB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34085940-80A7E950-E22B-4F19-8048-7E1FC44F15DB
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wasDerivedFrom
61b7857948ce987d08ce6304d1dc1b880d048694
P2860
Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus.