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Q34336279-6D352940-15B4-498D-8521-1DB026E900AE
Q34336279-6D352940-15B4-498D-8521-1DB026E900AE
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http://www.wikidata.org/entity/statement/Q34336279-6D352940-15B4-498D-8521-1DB026E900AE
Antisense oligonucleotides for the treatment of spinal muscular atrophy.
P2860
Q34336279-6D352940-15B4-498D-8521-1DB026E900AE
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34336279-6D352940-15B4-498D-8521-1DB026E900AE
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3278deb53a3a4a1b4f3c891279e01e6bd540fb66
P2860
Delivery of recombinant follistatin lessens disease severity in a mouse model of spinal muscular atrophy.