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Q35056714-DC608D1D-3B23-4B0C-904B-A67BA4B8C0CB
Q35056714-DC608D1D-3B23-4B0C-904B-A67BA4B8C0CB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35056714-DC608D1D-3B23-4B0C-904B-A67BA4B8C0CB
Vector design influences hepatic genotoxicity after adeno-associated virus gene therapy.
P2860
Q35056714-DC608D1D-3B23-4B0C-904B-A67BA4B8C0CB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35056714-DC608D1D-3B23-4B0C-904B-A67BA4B8C0CB
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Statement
wasDerivedFrom
4565fe7358fbae84da7989d1770891135f919ec5
P2860
Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)