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Q38091325-BCAFFACE-6635-4325-9F5F-2D7F37B89E40
Q38091325-BCAFFACE-6635-4325-9F5F-2D7F37B89E40
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38091325-BCAFFACE-6635-4325-9F5F-2D7F37B89E40
Current concepts in organic acidurias: understanding intra- and extracerebral disease manifestation.
P2860
Q38091325-BCAFFACE-6635-4325-9F5F-2D7F37B89E40
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38091325-BCAFFACE-6635-4325-9F5F-2D7F37B89E40
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wasDerivedFrom
9bf9acd76d1153e1780a13547465886a106de198
P2860
Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)