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Q38698489-04629F1B-8CC5-4C5D-8E8C-AFC9FAB1318A
Q38698489-04629F1B-8CC5-4C5D-8E8C-AFC9FAB1318A
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http://www.wikidata.org/entity/statement/Q38698489-04629F1B-8CC5-4C5D-8E8C-AFC9FAB1318A
Orkambi® and amplifier co-therapy improves function from a rare CFTR mutation in gene-edited cells and patient tissue.
P2860
Q38698489-04629F1B-8CC5-4C5D-8E8C-AFC9FAB1318A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38698489-04629F1B-8CC5-4C5D-8E8C-AFC9FAB1318A
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wasDerivedFrom
566086be8e1657c8f334e6d3aa99912fe8ff48fc
P2860
Functional Rescue of F508del-CFTR Using Small Molecule Correctors