about
Clinical development of gene therapy: results and lessons from recent successesIn utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical applicationProduction of lentiviral vectorsManufacturing of recombinant adeno-associated viral vectors for clinical trialsMethods and clinical development of adenovirus-vectored vaccines against mucosal pathogensFrom selection hits to clinical leads: progress in aptamer discoveryProduction and clinical development of nanoparticles for gene deliveryMoving oncolytic viruses into the clinic: clinical-grade production, purification, and characterization of diverse oncolytic virusesTargeted approaches to induce immune tolerance for Pompe disease therapyManufacturing of AcMNPV baculovirus vectors to enable gene therapy trialsMerging DBS with viral vector or stem cell implantation: "hybrid" stereotactic surgery as an evolution in the surgical treatment of Parkinson's diseaseBridging the gap: a second open-access sibling joins the MT family of journalsAllogeneic lymphocyte-licensed DCs expand T cells with improved antitumor activity and resistance to oxidative stress and immunosuppressive factorsMultiple mechanisms determine the sensitivity of human-induced pluripotent stem cells to the inducible caspase-9 safety switchProtein transduction therapy into cochleae via the round window niche in guinea pigs.Viral-mediated Ntf3 overexpression disrupts innervation and hearing in nondeafened guinea pig cochleaeAll-in-one processing of heterogeneous human cell grafts for gene and cell therapy.Ototoxicity-induced loss of hearing and inner hair cells is attenuated by HSP70 gene transfer.Proteomic profiling of salivary gland after nonviral gene transfer mediated by conventional plasmids and minicircles.The 2.8 Å Electron Microscopy Structure of Adeno-Associated Virus-DJ Bound by a Heparinoid Pentasaccharide.Toward a Rapid Production of Multivirus-Specific T Cells Targeting BKV, Adenovirus, CMV, and EBV from Umbilical Cord Blood.Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP GeneEngineering of GlcNAc-1-Phosphotransferase for Production of Highly Phosphorylated Lysosomal Enzymes for Enzyme Replacement Therapy.Toward Personalized Gene Therapy: Characterizing the Host Genetic Control of Lentiviral-Vector-Mediated Hepatic Gene Delivery.The Clonal Fate of Live Cells.Spatially and Temporally Regulated NRF2 Gene Therapy Using Mcp-1 Promoter in Retinal Ganglion Cell Injury.Efficient Production of Papillomavirus Gene Delivery Vectors in Defined In Vitro Reactions.Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett SyndromeIntegrase-Deficient Lentiviral Vector as an All-in-One Platform for Highly Efficient CRISPR/Cas9-Mediated Gene EditingImproved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery.Neuroglobin Can Prevent or Reverse Glaucomatous Progression in DBA/2J MiceCell Therapy in Myology: Dynamics of Muscle Precursor Cell Death after Intramuscular Administration in Non-human PrimatesPreclinical Evaluation of a Lentiviral Vector for Huntingtin Silencing.Lentivector Iterations and Pre-Clinical Scale-Up/Toxicity Testing: Targeting Mobilized CD34+ Cells for Correction of Fabry DiseaseSingle Cell-Based Vector Tracing in Patients with ADA-SCID Treated with Stem Cell Gene Therapy.In Vivo Murine-Matured Human CD3+ Cells as a Preclinical Model for T Cell-Based Immunotherapies.Anti-high Mobility Group Box 1 Antibody Ameliorates Albuminuria in MRL/lpr Lupus-Prone Mice.Public Attitudes toward Gene Therapy in China.Mesenchymal Stem Cells Overexpressing Interleukin-10 Promote Neuroprotection in Experimental Acute Ischemic Stroke.Marmosets as a preclinical model for testing "off-label" use of doxycycline to turn on Flt3L expression from high-capacity adenovirus vectors.
P1433
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P1433
description
revista científica
@es
revue scientifique
@fr
rivista scientifica
@it
scientific journal
@en
wetenschappelijk tijdschrift van Cell Press
@nl
wissenschaftliche Fachzeitschrift
@de
науковий журнал
@uk
name
Molecular Therapy. Methods & Clinical Development
@ast
Molecular Therapy. Methods & Clinical Development
@de
Molecular Therapy. Methods & Clinical Development
@en
Molecular Therapy. Methods & Clinical Development
@es
Molecular Therapy. Methods & Clinical Development
@fr
Molecular therapy. Methods & clinical development
@nl
type
label
Molecular Therapy. Methods & Clinical Development
@ast
Molecular Therapy. Methods & Clinical Development
@de
Molecular Therapy. Methods & Clinical Development
@en
Molecular Therapy. Methods & Clinical Development
@es
Molecular Therapy. Methods & Clinical Development
@fr
Molecular therapy. Methods & clinical development
@nl
altLabel
Mol Ther Methods Clin Dev
@en
Molecular Therapy: Methods & Clinical Development
@en
prefLabel
Molecular Therapy. Methods & Clinical Development
@ast
Molecular Therapy. Methods & Clinical Development
@de
Molecular Therapy. Methods & Clinical Development
@en
Molecular Therapy. Methods & Clinical Development
@es
Molecular Therapy. Methods & Clinical Development
@fr
Molecular therapy. Methods & clinical development
@nl
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Molecular Therapy. Methods & Clinical Development
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