Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome
about
Improved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery.Radically truncated MeCP2 rescues Rett syndrome-like neurological defects.Site-directed RNA repair of endogenous Mecp2 RNA in neurons.Recent progress and considerations for AAV gene therapies targeting the central nervous system.Rett syndrome from bench to bedside: recent advances.Autism spectrum disorder: prospects for treatment using gene therapy.Genomics in neurodevelopmental disorders: an avenue to personalized medicine
P2860
Q33655727-09395C94-87C1-4DF0-BD70-6B9C9ADF34B2Q41919307-03D2DA2E-CEBA-4257-9BAC-4952A5D2454AQ47594202-988B2E19-3E0A-4624-87EF-05C7704A7378Q54206545-722F7FE4-77D5-4612-96DD-93159E1793C4Q55312256-C7912636-F58F-4DEF-BC54-99FA39BECACCQ55339450-DDC1FBA0-34EB-4876-8B5A-261F2EC9DEFCQ58797492-E2AC30C3-6650-4931-A2F3-2FD71209C0A6
P2860
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome
description
2017 nî lūn-bûn
@nan
2017 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2017 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
name
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@ast
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@en
type
label
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@ast
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@en
prefLabel
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@ast
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@en
P2093
P2860
P50
P1476
Development of a Novel AAV Gen ...... a Mouse Model of Rett Syndrome
@en
P2093
Noha G Bahey
Sarah Sinnett
Steven J Gray
Stuart R Cobb
Thishnapha Vudhironarit
P2860
P304
P356
10.1016/J.OMTM.2017.04.007
P577
2017-04-22T00:00:00Z