A simplified baculovirus-AAV expression vector system coupled with one-step affinity purification yields high-titer rAAV stocks from insect cells
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Preclinical safety of RNAi-mediated HTT suppression in the rhesus macaque as a potential therapy for Huntington's diseaseManufacturing of recombinant adeno-associated viral vectors for clinical trialsDynamics of Ionic Shifts in Cortical Spreading Depression.Causal Interrogation of Neuronal Networks and Behavior through Virally Transduced Ivermectin Receptors.Cell-type specific expression of the vasopressin gene analyzed by AAV mediated gene delivery of promoter deletion constructs into the rat SON in vivoNeural basis of benzodiazepine reward: requirement for α2 containing GABAA receptors in the nucleus accumbens.Cell-type specific oxytocin gene expression from AAV delivered promoter deletion constructs into the rat supraoptic nucleus in vivo.SCHEMA computational design of virus capsid chimeras: calibrating how genome packaging, protection, and transduction correlate with calculated structural disruption.Scalable downstream strategies for purification of recombinant adeno- associated virus vectors in light of the properties.Producing recombinant adeno-associated virus in foster cells: overcoming production limitations using a baculovirus-insect cell expression strategy.Gene therapy prolongs survival and restores function in murine and canine models of myotubular myopathy.Forelimb treatment in a large cohort of dystrophic dogs supports delivery of a recombinant AAV for exon skipping in Duchenne patients.Evaluation of an AAV2-based rapamycin-regulated glial cell line-derived neurotrophic factor (GDNF) expression vector system.Chondroitin Sulfate is the Primary Receptor for a Peptide-Modified AAV That Targets Brain Vascular Endothelium In Vivo.Large-scale recombinant adeno-associated virus productionGenetic therapies for cystic fibrosis lung diseaseNeuroprotection by rAAV-mediated gene transfer of bone morphogenic protein 7Reproducible high yields of recombinant adeno-associated virus produced using invertebrate cells in 0.02- to 200-liter cultures.AAV-mediated in vivo knockdown of luciferase using combinatorial RNAi and U1i.AAV's Golden Jubilee.Long-term restoration of cardiac dystrophin expression in golden retriever muscular dystrophy following rAAV6-mediated exon skippingVersatile and efficient genome editing in human cells by combining zinc-finger nucleases with adeno-associated viral vectors.Serum proteomic profiling reveals fragments of MYOM3 as potential biomarkers for monitoring the outcome of therapeutic interventions in muscular dystrophies.Human galectin 3 binding protein interacts with recombinant adeno-associated virus type 6Ultracentrifugation-free chromatography-mediated large-scale purification of recombinant adeno-associated virus serotype 1 (rAAV1).Progress and challenges in viral vector manufacturingBaculovirus: an insect-derived vector for diverse gene transfer applicationsAdvanced Characterization of DNA Molecules in rAAV Vector Preparations by Single-stranded Virus Next-generation Sequencing.A concept of eliminating nonhomologous recombination for scalable and safe AAV vector generation for human gene therapySubretinal gene therapy of mice with Bardet-Biedl syndrome type 1.OneBac: platform for scalable and high-titer production of adeno-associated virus serotype 1-12 vectors for gene therapyIntrajugular vein delivery of AAV9-RNAi prevents neuropathological changes and weight loss in Huntington's disease mice.AAV-mediated gene therapy for liver diseases: the prime candidate for clinical application?Biotechnological applications of recombinant single-domain antibody fragments.Downstream processing of cell culture-derived virus particles.Use of bacterial artificial chromosomes in baculovirus research and recombinant protein expression: current trends and future perspectives.Peptide affinity reagents for AAV capsid recognition and purificationThe baculovirus expression vector system: A commercial manufacturing platform for viral vaccines and gene therapy vectors.New approaches to gene and cell therapy for hemophilia.Deletion of Aquaporin-4 Curtails Extracellular Glutamate Elevation in Cortical Spreading Depression in Awake Mice.
P2860
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P2860
A simplified baculovirus-AAV expression vector system coupled with one-step affinity purification yields high-titer rAAV stocks from insect cells
description
2009 nî lūn-bûn
@nan
2009 թուականի Յունիսին հրատարակուած գիտական յօդուած
@hyw
2009 թվականի հունիսին հրատարակված գիտական հոդված
@hy
2009年の論文
@ja
2009年論文
@yue
2009年論文
@zh-hant
2009年論文
@zh-hk
2009年論文
@zh-mo
2009年論文
@zh-tw
2009年论文
@wuu
name
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@ast
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@en
type
label
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@ast
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@en
prefLabel
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@ast
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@en
P2093
P2860
P356
P1433
P1476
A simplified baculovirus-AAV e ...... rAAV stocks from insect cells
@en
P2093
Justin R Levy
Richard H Smith
Robert M Kotin
P2860
P304
P356
10.1038/MT.2009.128
P577
2009-06-16T00:00:00Z