Gene therapy rescues cone structure and function in the 3-month-old rd12 mouse: a model for midcourse RPE65 leber congenital amaurosis
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Clinical development of gene therapy: results and lessons from recent successesLipid Nanoparticles for Ocular Gene DeliveryGene therapy: light is finally in the tunnelAAV-mediated gene therapy in mouse models of recessive retinal degenerationA comprehensive review of retinal gene therapyAAV-mediated cone rescue in a naturally occurring mouse model of CNGA3-achromatopsiaThe human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina.Differential proteomics and functional research following gene therapy in a mouse model of Leber congenital amaurosisDiscovery Genetics - The History and Future of Spontaneous Mutation Research.C1q enhances cone photoreceptor survival in a mouse model of autosomal recessive retinitis pigmentosa.iTRAQ-Based Proteomic Analysis of Visual Cycle-Associated Proteins in RPE of rd12 Mice before and after RPE65 Gene Delivery.Histone Deacetylases Inhibitors in the Treatment of Retinal Degenerative Diseases: Overview and PerspectivesTrans-Corneal Subretinal Injection in Mice and Its Effect on the Function and Morphology of the Retina.Effects of Subretinal Gene Transfer at Different Time Points in a Mouse Model of Retinal Degeneration.It's never too late to save a photoreceptor.Prospectives for gene therapy of retinal degenerationsHuman retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvementAAV-mediated gene therapy in the guanylate cyclase (RetGC1/RetGC2) double knockout mouse model of Leber congenital amaurosis.S/MAR-containing DNA nanoparticles promote persistent RPE gene expression and improvement in RPE65-associated LCAMid-stage intervention achieves similar efficacy as conventional early-stage treatment using gene therapy in a pre-clinical model of retinitis pigmentosaThe Degeneration and Apoptosis Patterns of Cone Photoreceptors in rd11 Mice.AAV-mediated lysophosphatidylcholine acyltransferase 1 (Lpcat1) gene replacement therapy rescues retinal degeneration in rd11 mice.SLC7A14 linked to autosomal recessive retinitis pigmentosa.The Rpe65 rd12 allele exerts a semidominant negative effect on vision in miceGene therapy for retinal diseaseStem cells for investigation and treatment of inherited retinal disease.Age-related changes in Cngb1-X1 knockout mice: prolonged cone survival.Gene-based Therapy in a Mouse Model of Blue Cone Monochromacy.Retinal gene therapy using adeno-associated viral vectors: multiple applications for a small virus.Long-term retinal cone rescue using a capsid mutant AAV8 vector in a mouse model of CNGA3-achromatopsia.Recent Advancements in Gene Therapy for Hereditary Retinal Dystrophies.
P2860
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P2860
Gene therapy rescues cone structure and function in the 3-month-old rd12 mouse: a model for midcourse RPE65 leber congenital amaurosis
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2011 nî lūn-bûn
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2011 թուականի Յունուարին հրատարակուած գիտական յօդուած
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2011 թվականի հունվարին հրատարակված գիտական հոդված
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2011年の論文
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2011年学术文章
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2011年学术文章
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2011年学术文章
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2011年学术文章
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name
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@ast
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@en
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@nl
type
label
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@ast
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@en
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@nl
prefLabel
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@ast
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@en
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@nl
P2093
P2860
P356
P1476
Gene therapy rescues cone stru ...... E65 leber congenital amaurosis
@en
P2093
Bärbel Rohrer
Fansheng Kong
Ji-jing Pang
Qinxiang Zheng
Wensheng Li
William W Hauswirth
P2860
P356
10.1167/IOVS.10-6138
P407
P577
2011-01-05T00:00:00Z