The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver.
about
Role of the vector genome and underlying factor IX mutation in immune responses to AAV gene therapy for hemophilia BSelf-complementary AAVs induce more potent transgene product-specific immune responses compared to a single-stranded genomeThe interplay of post-translational modification and gene therapyDevelopments in the treatment of hemophilia B: focus on emerging gene therapyGene therapy for hemophiliaLiver-targeted gene therapy: Approaches and challengesEngineering antibody-like inhibitors to prevent and treat HIV-1 infection.Immune tolerance induction to factor IX through B cell gene transfer: TLR9 signaling delineates between tolerogenic and immunogenic B cells.Influence of immune responses in gene/stem cell therapies for muscular dystrophies.Cell-Mediated Immunity to AAV Vectors, Evolving Concepts and Potential Solutions.Adeno-associated virus (AAV) vectors in gene therapy: immune challenges and strategies to circumvent them.Activation of the cellular unfolded protein response by recombinant adeno-associated virus vectors.Intraganglionic AAV6 results in efficient and long-term gene transfer to peripheral sensory nervous system in adult rats.Development of Gene Transfer for Induction of Antigen-specific Tolerance.Perinatal gene transfer to the liver.Self-complementary adeno-associated viral vectors for gene therapy of hemophilia B: progress and challengesUnique Roles of TLR9- and MyD88-Dependent and -Independent Pathways in Adaptive Immune Responses to AAV-Mediated Gene TransferAdeno-associated virus activates an innate immune response in normal human cells but not in osteosarcoma cells.Pharmacological modulation of humoral immunity in a nonhuman primate model of AAV gene transfer for hemophilia B.MyD88 signaling in B cells regulates the production of Th1-dependent antibodies to AAVThe threefold protrusions of adeno-associated virus type 8 are involved in cell surface targeting as well as postattachment processing.An acidic oligopeptide displayed on AAV2 improves axial muscle tropism after systemic delivery.Gene Therapy for Duchenne muscular dystrophy.Deficiency in MyD88 Signaling Results in Decreased Antibody Responses to an Adeno-Associated Virus Vector in Murine Pompe Disease.Preclinical evaluation of an anti-HCV miRNA cluster for treatment of HCV infectionEngineered AAV vector minimizes in vivo targeting of transduced hepatocytes by capsid-specific CD8+ T cells.Differential type I interferon-dependent transgene silencing of helper-dependent adenoviral vs. adeno-associated viral vectors in vivo.RNA Interference Mediated Interleukin-1β Silencing in Inflamed Chondrocytes Decreases Target and Downstream Catabolic Responses.Serotype-specific Binding Properties and Nanoparticle Characteristics Contribute to the Immunogenicity of rAAV1 VectorsAdvanced Characterization of DNA Molecules in rAAV Vector Preparations by Single-stranded Virus Next-generation Sequencing.CpG-depleted adeno-associated virus vectors evade immune detection.IL12-mediated liver inflammation reduces the formation of AAV transcriptionally active forms but has no effect over preexisting AAV transgene expression.Immune responses to AAV vectors: overcoming barriers to successful gene therapySuperior In vivo Transduction of Human Hepatocytes Using Engineered AAV3 Capsid.Targeted modifications in adeno-associated virus serotype 8 capsid improves its hepatic gene transfer efficiency in vivoA review of therapeutic prospects of non-viral gene therapy in the retinal pigment epitheliumGene Therapy for the Treatment of Neurological Disorders: Metabolic Disorders.Recombinant adeno-associated virus vectors in the treatment of rare diseases.AAV Vectors Vaccines Against Infectious Diseases.Promise and problems associated with the use of recombinant AAV for the delivery of anti-HIV antibodies
P2860
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P2860
The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver.
description
2011 nî lūn-bûn
@nan
2011 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2011 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2011年の論文
@ja
2011年論文
@yue
2011年論文
@zh-hant
2011年論文
@zh-hk
2011年論文
@zh-mo
2011年論文
@zh-tw
2011年论文
@wuu
name
The genome of self-complementa ...... immune responses in the liver.
@ast
The genome of self-complementa ...... immune responses in the liver.
@en
type
label
The genome of self-complementa ...... immune responses in the liver.
@ast
The genome of self-complementa ...... immune responses in the liver.
@en
prefLabel
The genome of self-complementa ...... immune responses in the liver.
@ast
The genome of self-complementa ...... immune responses in the liver.
@en
P2093
P2860
P1433
P1476
The genome of self-complementa ...... immune responses in the liver.
@en
P2093
Ashley T Martino
Babak Moghimi
Brendan Lee
Daniel A Muruve
David M Markusic
Hildegund C J Ertl
Irene Zolotukhin
Masataka Suzuki
Renee C Ryals
Roland W Herzog
P2860
P304
P356
10.1182/BLOOD-2010-10-314518
P407
P577
2011-04-07T00:00:00Z