Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
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Multi-parametric MRI at 14T for muscular dystrophy mice treated with AAV vector-mediated gene therapyNon-invasive MRI and spectroscopy of mdx mice reveal temporal changes in dystrophic muscle imaging and in energy deficitsSkeletal Muscle Quantitative Nuclear Magnetic Resonance Imaging and Spectroscopy as an Outcome Measure for Clinical TrialsHomozygous nonsense mutation in SGCA is a common cause of limb-girdle muscular dystrophy in Assiut, Egypt.Sustained alpha-sarcoglycan gene expression after gene transfer in limb-girdle muscular dystrophy, type 2D.Changes in muscle T2 and tissue damage after downhill running in mdx mice.Quantitative T2 combined with texture analysis of nuclear magnetic resonance images identify different degrees of muscle involvement in three mouse models of muscle dystrophy: mdx, Largemyd and mdx/Largemyd.Genome-wide identification of FoxO-dependent gene networks in skeletal muscle during C26 cancer cachexia.Long-term systemic myostatin inhibition via liver-targeted gene transfer in golden retriever muscular dystrophy.Recent developments in the treatment of Duchenne muscular dystrophy and spinal muscular atrophy.Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle.Vascular Regeneration in Ischemic Hindlimb by Adeno-Associated Virus Expressing Conditionally Silenced Vascular Endothelial Growth FactorOverexpression of Galgt2 reduces dystrophic pathology in the skeletal muscles of alpha sarcoglycan-deficient micemiRNAS in normal and diseased skeletal muscle.Evaluation of vascular delivery methodologies to enhance rAAV6-mediated gene transfer to canine striated musculature.AAV-directed muscular dystrophy gene therapy.Cell-matrix interactions in muscle disease.Neprilysin gene transfer: A promising therapeutic approach for Alzheimer's disease.RNA interference improves myopathic phenotypes in mice over-expressing FSHD region gene 1 (FRG1).Contrast-Enhanced Near-Infrared Optical Imaging Detects Exacerbation and Amelioration of Murine Muscular Dystrophy.
P2860
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P2860
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
description
2007 nî lūn-bûn
@nan
2007年の論文
@ja
2007年学术文章
@wuu
2007年学术文章
@zh
2007年学术文章
@zh-cn
2007年学术文章
@zh-hans
2007年学术文章
@zh-my
2007年学术文章
@zh-sg
2007年學術文章
@yue
2007年學術文章
@zh-hant
name
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@en
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@nl
type
label
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@en
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@nl
prefLabel
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@en
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@nl
P2093
P356
P1433
P1476
Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.
@en
P2093
Barry J Byrne
Cathryn S Mah
Christina A Pacak
Gabe Gaidosh
Glenn A Walter
Kevin P Campbell
Nathan Bryant
Sean Germain
P304
P356
10.1038/SJ.MT.6300246
P577
2007-07-24T00:00:00Z