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Q33652467-3BAF5609-5A9C-4B3D-A737-5AC839566503
Q33652467-3BAF5609-5A9C-4B3D-A737-5AC839566503
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33652467-3BAF5609-5A9C-4B3D-A737-5AC839566503
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome
P2860
Q33652467-3BAF5609-5A9C-4B3D-A737-5AC839566503
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33652467-3BAF5609-5A9C-4B3D-A737-5AC839566503
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
a3609218600f69935db49a657fca152b9bd01d41
P2860
Novel Vector Design and Hexosaminidase Variant Enabling Self-Complementary Adeno-Associated Virus for the Treatment of Tay-Sachs Disease.