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GT.2016.53
GT.2016.53
http://dx.doi.org/10.1038/GT.2016.53
Long-term, high-level hepatic secretion of acid α-glucosidase for Pompe disease achieved in non-human primates using helper-dependent adenovirus.
P356
Q38846270-B102D64C-DFEA-4D98-AAFB-F255081CF91C
P356
GT.2016.53
http://dx.doi.org/10.1038/GT.2016.53