Long-term, high-level hepatic secretion of acid α-glucosidase for Pompe disease achieved in non-human primates using helper-dependent adenovirus.
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Gene therapy for monogenic liver diseases: clinical successes, current challenges and future prospects.Gene therapy with helper-dependent adenoviral vectors: lessons from studies in large animal models.AAV-mediated transcription factor EB (TFEB) gene delivery ameliorates muscle pathology and function in the murine model of Pompe Disease.Current and Future Treatments for Lysosomal Storage Disorders.
P2860
Long-term, high-level hepatic secretion of acid α-glucosidase for Pompe disease achieved in non-human primates using helper-dependent adenovirus.
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Long-term, high-level hepatic ...... g helper-dependent adenovirus.
@en
type
label
Long-term, high-level hepatic ...... g helper-dependent adenovirus.
@en
prefLabel
Long-term, high-level hepatic ...... g helper-dependent adenovirus.
@en
P2093
P2860
P356
P1433
P1476
Long-term, high-level hepatic ...... ng helper-dependent adenovirus
@en
P2093
A Amalfitano
C Pereria-Hicks
D P W Rastall
S Godbehere-Roosa
S S Seregin
P2860
P2888
P304
P356
10.1038/GT.2016.53
P50
P577
2016-07-01T00:00:00Z