Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs - Wikidata - wikimedia - TriplyDB

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

http://www.wikidata.org/entity/Q24569504

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Inhibition of HIV-1 multiplication by antisense U7 snRNAs and siRNAs targeting cyclophilin A Lipid-based Transfection Reagents Exhibit Cryo-induced Increase in Transfection Efficiency.Progress toward therapy with antisense-mediated splicing modulation Doxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettes Antisense Oligonucleotides Promote Exon Inclusion and Correct the Common c.-32-13T>G GAA Splicing Variant in Pompe Disease Future alternative therapies for β-thalassemia.Producing recombinant adeno-associated virus in foster cells: overcoming production limitations using a baculovirus-insect cell expression strategy.Enhancement of β-Globin Gene Expression in Thalassemic IVS2-654 Induced Pluripotent Stem Cell-Derived Erythroid Cells by Modified U7 snRNA.Chimeric snRNA molecules carrying antisense sequences against the splice junctions of exon 51 of the dystrophin pre-mRNA induce exon skipping and restoration of a dystrophin synthesis in Delta 48-50 DMD cells Forelimb treatment in a large cohort of dystrophic dogs supports delivery of a recombinant AAV for exon skipping in Duchenne patients.Sensitivity of splice sites to antisense oligonucleotides in vivo.The status of exon skipping as a therapeutic approach to duchenne muscular dystrophy Repair of pre-mRNA splicing: prospects for a therapy for spinal muscular atrophy.Duchenne muscular dystrophy gene therapy in the canine model.mRNA transcript diversity creates new opportunities for pharmacological intervention.MRI roadmap-guided transendocardial delivery of exon-skipping recombinant adeno-associated virus restores dystrophin expression in a canine model of Duchenne muscular dystrophy.Exon skipping as a therapeutic strategy applied to an RYR1 mutation with pseudo-exon inclusion causing a severe core myopathy.AAV vectors for RNA-based modulation of gene expression.Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy.Lessons from non-canonical splicing Micro-minicircle Gene Therapy: Implications of Size on Fermentation, Complexation, Shearing Resistance, and Expression.Alternative splicing: role of pseudoexons in human disease and potential therapeutic strategies.Targeting the splicing of mRNA in autoimmune diseases: BAFF inhibition in Sjögren's syndrome as a proof of concept Gene therapy in thalassemia and hemoglobinopathies.RNA splicing: disease and therapy.Viral Vector-Mediated Antisense Therapy for Genetic Diseases.Analysis of the functional consequences of targeted exon deletion in COL7A1 reveals prospects for dystrophic epidermolysis bullosa therapy.Localizing the RPGR protein along the cilium: a new method to determine efficacies to treat RPGR mutations.The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery.Intracellular generation of single-stranded DNA for chromosomal triplex formation and induced recombination.Antisense oligonucleotides with different backbones. Modification of splicing pathways and efficacy of uptake.Muscle function recovery in golden retriever muscular dystrophy after AAV1-U7 exon skipping.Double-target Antisense U1snRNAs Correct Mis-splicing Due to c.639+861C>T and c.639+919G>A GLA Deep Intronic Mutations.Dystrophin rescue by trans-splicing: a strategy for DMD genotypes not eligible for exon skipping approaches Variants of U1 small nuclear RNA assemble into spliceosomal complexes.An exon-specific U1 small nuclear RNA (snRNA) strategy to correct splicing defects.Correction of aberrant splicing of the cystic fibrosis transmembrane conductance regulator (CFTR) gene by antisense oligonucleotides.Inhibition of collagen alpha 1(I) expression by the 5' stem-loop as a molecular decoy.RNA-Seq Analysis of an Antisense Sequence Optimized for Exon Skipping in Duchenne Patients Reveals No Off-Target Effect.

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P2860

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

http://www.wikidata.org/entity/Q24569504

description

1998 nî lūn-bûn

@nan

1998 թուականի Ապրիլին հրատարակուած գիտական յօդուած

@hyw

1998 թվականի ապրիլին հրատարակված գիտական հոդված

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1998年の論文

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1998年論文

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1998年論文

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1998年論文

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1998年論文

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1998年論文

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1998年论文

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name

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@ast

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@en

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@nl

type

label

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@ast

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@en

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@nl

prefLabel

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@ast

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@en

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@nl

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Proceedings of the National Academy of Sciences of the United States of America

P1476

Stable alteration of pre-mRNA splicing patterns by modified U7 small nuclear RNAs

@en

P2093

D Suter

http://www.w3.org/2001/XMLSchema#string

L Gorman

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R Kole

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V Emerick

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P2860

The Sm binding site targets U7 snRNA to coiled bodies (spheres) of amphibian oocytes.

Two-step affinity purification of U7 small nuclear ribonucleoprotein particles using complementary biotinylated 2'-O-methyl oligoribonucleotides

Restoration of correct splicing in thalassemic pre-mRNA by antisense oligonucleotides

The low abundance of U7 snRNA is partly determined by its Sm binding site

3' end processing of mouse histone pre-mRNA: evidence for additional base-pairing between U7 snRNA and pre-mRNA

Assembly, nuclear import and function of U7 snRNPs studied by microinjection of synthetic U7 RNA into Xenopus oocytes

Tricine-sodium dodecyl sulfate-polyacrylamide gel electrophoresis for the separation of proteins in the range from 1 to 100 kDa

Multiple processing-defective mutations in a mammalian histone pre-mRNA are suppressed by compensatory changes in U7 RNA both in vivo and in vitro

Direct selection for mutations affecting specific splice sites in a hamster dihydrofolate reductase minigene

The mutational spectrum of single base-pair substitutions in mRNA splice junctions of human genes: causes and consequences

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4929-4934

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2818624

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10.1073/PNAS.95.9.4929

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9

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13720640

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9560205

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20190

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