MRI roadmap-guided transendocardial delivery of exon-skipping recombinant adeno-associated virus restores dystrophin expression in a canine model of Duchenne muscular dystrophy.
about
Dystrophin-deficient large animal models: translational research and exon skippingAnimal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapyRescue of cardiomyopathy through U7snRNA-mediated exon skipping in Mybpc3-targeted knock-in miceTracking of stem cells in vivo for cardiovascular applications.Quantitative NMRI and NMRS identify augmented disease progression after loss of ambulation in forearms of boys with Duchenne muscular dystrophy.Forelimb treatment in a large cohort of dystrophic dogs supports delivery of a recombinant AAV for exon skipping in Duchenne patients.Progress and prospects of gene therapy clinical trials for the muscular dystrophies.Duchenne muscular dystrophy gene therapy in the canine model.Prospect of gene therapy for cardiomyopathy in hereditary muscular dystrophy.100-fold but not 50-fold dystrophin overexpression aggravates electrocardiographic defects in the mdx model of Duchenne muscular dystrophy.Missing links in cardiology: long non-coding RNAs enter the arena.Drug Discovery of Therapies for Duchenne Muscular Dystrophy.Nanotherapy for Duchenne muscular dystrophy.Muscle function recovery in golden retriever muscular dystrophy after AAV1-U7 exon skipping.Dystrophin rescue by trans-splicing: a strategy for DMD genotypes not eligible for exon skipping approaches
P2860
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P2860
MRI roadmap-guided transendocardial delivery of exon-skipping recombinant adeno-associated virus restores dystrophin expression in a canine model of Duchenne muscular dystrophy.
description
2012 nî lūn-bûn
@nan
2012年の論文
@ja
2012年論文
@yue
2012年論文
@zh-hant
2012年論文
@zh-hk
2012年論文
@zh-mo
2012年論文
@zh-tw
2012年论文
@wuu
2012年论文
@zh
2012年论文
@zh-cn
name
MRI roadmap-guided transendoca ...... f Duchenne muscular dystrophy.
@ast
MRI roadmap-guided transendoca ...... f Duchenne muscular dystrophy.
@en
type
label
MRI roadmap-guided transendoca ...... f Duchenne muscular dystrophy.
@ast
MRI roadmap-guided transendoca ...... f Duchenne muscular dystrophy.
@en
prefLabel
MRI roadmap-guided transendoca ...... f Duchenne muscular dystrophy.
@ast
MRI roadmap-guided transendoca ...... f Duchenne muscular dystrophy.
@en
P2093
P2860
P356
P1433
P1476
MRI roadmap-guided transendoca ...... of Duchenne muscular dystrophy
@en
P2093
A Z Faranesh
I M Barbash
J N Kornegay
S Cecchini
P2860
P2888
P304
P356
10.1038/GT.2012.38
P577
2012-05-03T00:00:00Z