Therapeutic response in feline sandhoff disease despite immunity to intracranial gene therapy. - Wikidata - wikimedia - TriplyDB

Therapeutic response in feline sandhoff disease despite immunity to intracranial gene therapy.

Therapeutic response in feline sandhoff disease despite immunity to intracranial gene therapy.

http://www.wikidata.org/entity/Q30541192

about

Animal models of GM2 gangliosidosis: utility and limitations Biomarkers for disease progression and AAV therapeutic efficacy in feline Sandhoff disease High resolution MRI anatomy of the cat brain at 3 Tesla.Sustained normalization of neurological disease after intracranial gene therapy in a feline model.Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy Gene therapy for the nervous system: challenges and new strategies.A review of gene therapy in canine and feline models of lysosomal storage disorders.In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy AAV-mediated gene delivery in a feline model of Sandhoff disease corrects lysosomal storage in the central nervous system.Protease-resistant modified human β-hexosaminidase B ameliorates symptoms in GM2 gangliosidosis model Enhancement by Uridine Diphosphate of Macrophage Inflammatory Protein-1 Alpha Production in Microglia Derived from Sandhoff Disease Model Mice.Reversibility of neuropathology in Tay-Sachs-related diseases.Gene therapy for the neurological manifestations in lysosomal storage disorders.Sphingolipid lysosomal storage disorders.Adeno-Associated Virus-Based Gene Therapy for CNS Diseases.AAV-mediated gene delivery attenuates neuroinflammation in feline Sandhoff disease.Intracisternal delivery of AAV9 results in oligodendrocyte and motor neuron transduction in the whole central nervous system of cats.Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model.Direct Intracranial Injection of AAVrh8 Encoding Monkey β-N-Acetylhexosaminidase Causes Neurotoxicity in the Primate Brain.Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease.AAVrh10 gene therapy ameliorates central and peripheral nervous system disease in canine globoid cell leukodystrophy (Krabbe disease).

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P2860

Therapeutic response in feline sandhoff disease despite immunity to intracranial gene therapy.

http://www.wikidata.org/entity/Q30541192

description

2013 nî lūn-bûn

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2013 թուականի Մայիսին հրատարակուած գիտական յօդուած

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2013 թվականի մայիսին հրատարակված գիտական հոդված

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2013年の論文

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2013年論文

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2013年論文

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2013年論文

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2013年論文

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2013年論文

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2013年论文

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name

Therapeutic response in feline ...... to intracranial gene therapy.

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Therapeutic response in feline ...... to intracranial gene therapy.

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type

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Therapeutic response in feline ...... to intracranial gene therapy.

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Therapeutic response in feline ...... to intracranial gene therapy.

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Therapeutic response in feline ...... to intracranial gene therapy.

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Therapeutic response in feline ...... to intracranial gene therapy.

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Molecular Therapy

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Therapeutic response in feline ...... y to intracranial gene therapy

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Aime K Johnson

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Allison M Bradbury

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Ashley N Randle

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Brandon L Brunson

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Douglas R Martin

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Heather Gray-Edwards

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Henry J Baker

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Laura S Jackson

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M Begona Cachón-González

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Miguel Sena-Esteves

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P2860

DNAWorks: an automated method for designing oligonucleotides for PCR-based gene synthesis

A simple method for the isolation and purification of total lipides from animal tissues

Adenoviral gene therapy of the Tay-Sachs disease in hexosaminidase A-deficient knock-out mice

In vivo protein transduction: delivery of a biologically active protein into the mouse

Effective gene therapy in an authentic model of Tay-Sachs-related diseases

Gene transfer corrects acute GM2 gangliosidosis--potential therapeutic contribution of perivascular enzyme flow

Aberrant sprouting and downregulation of tyrosine hydroxylase in lesioned nigrostriatal dopamine neurons induced by long-lasting overexpression of glial cell line derived neurotrophic factor in the striatum by lentiviral gene transfer.

Thymic alterations in GM2 gangliosidoses model mice.

Molecular consequences of the pathogenic mutation in feline GM1 gangliosidosis

Efficient neuronal gene transfer with AAV8 leads to neurotoxic levels of tau or green fluorescent proteins.

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1306-1315

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scholarly article

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10.1038/MT.2013.86

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7

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21

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Thomas N Seyfried

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2013-05-21T00:00:00Z

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236923849

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