Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy.
about
Gait disturbances in dystrophic hamsters.Role of cyclic AMP-dependent kinase response element-binding protein in recombinant adeno-associated virus-mediated transduction of heart muscle cells.Efficient retrograde transport of adeno-associated virus type 8 to spinal cord and dorsal root ganglion after vector delivery in muscle.Amelioration of laminin-alpha2-deficient congenital muscular dystrophy by somatic gene transfer of miniagrin.Naloxone can act as an analgesic agent without measurable chronic side effects in mice with a mutant mu-opioid receptor expressed in different sites of pain pathway.Novel approaches to treat muscular dystrophies.Harnessing the potential of dystrophin-related proteins for ameliorating Duchenne's muscular dystrophy.Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives.Adenovirus mediated gene transfer to skeletal muscle.Post-Natal knockdown of fukutin-related protein expression in muscle by long-termRNA interference induces dystrophic pathology [corrected]Reversal of RNA missplicing and myotonia after muscleblind overexpression in a mouse poly(CUG) model for myotonic dystrophy.Non-viral gene delivery in skeletal muscle: a protein factory.Respiratory muscle fibres: specialisation and plasticity.Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model.Sarcoglycanopathies: molecular pathogenesis and therapeutic prospectsImproved function of the failing rat heart by regulated expression of insulin-like growth factor I via intramuscular gene transfer.Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD).Alpha1-syntrophin-deficient skeletal muscle exhibits hypertrophy and aberrant formation of neuromuscular junctions during regeneration.Gene therapy approaches for stem cell protection.Safety and in vivo expression of a GNE-transgene: a novel treatment approach for hereditary inclusion body myopathy-2.AAV-directed muscular dystrophy gene therapy.Cell-matrix interactions in muscle disease.An inhibitor of transforming growth factor beta type I receptor ameliorates muscle atrophy in a mouse model of caveolin 3-deficient muscular dystrophy.Successful interference with cellular immune responses to immunogenic proteins encoded by recombinant viral vectors.Feasibility of generating adeno-associated virus packaging cell lines containing inducible adenovirus helper genes.A novel gene expression control system and its use in stable, high-titer 293 cell-based adeno-associated virus packaging cell lines.Muscle and heart function restoration in a limb girdle muscular dystrophy 2I (LGMD2I) mouse model by systemic FKRP gene delivery.Cardiomyocyte-specific gene expression following recombinant adeno-associated viral vector transduction.Analysis of the spatial, temporal and tissue-specific transcription of gamma-sarcoglycan gene using a transgenic mouse.Developmental Changes in the ECG of a Hamster Model of Muscular Dystrophy and Heart Failure.Protein trans-splicing as a means for viral vector-mediated in vivo gene therapy.Fiber composition and oxidative capacity of hamster skeletal muscle.Efficient and long-term intracardiac gene transfer in delta-sarcoglycan-deficiency hamster by adeno-associated virus-2 vectors.Long-term expression and repeated administration of AAV type 1, 2 and 5 vectors in skeletal muscle of immunocompetent adult mice.Microbubble ultrasound improves the efficiency of gene transduction in skeletal muscle in vivo with reduced tissue damage.A canine minidystrophin is functional and therapeutic in mdx mice.Deficiency of alpha-sarcoglycan differently affects fast- and slow-twitch skeletal muscles.
P2860
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P2860
Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy.
description
2000 nî lūn-bûn
@nan
2000 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2000 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2000年の論文
@ja
2000年論文
@yue
2000年論文
@zh-hant
2000年論文
@zh-hk
2000年論文
@zh-mo
2000年論文
@zh-tw
2000年论文
@wuu
name
Full functional rescue of a co ...... vector-directed gene therapy.
@ast
Full functional rescue of a co ...... vector-directed gene therapy.
@en
type
label
Full functional rescue of a co ...... vector-directed gene therapy.
@ast
Full functional rescue of a co ...... vector-directed gene therapy.
@en
prefLabel
Full functional rescue of a co ...... vector-directed gene therapy.
@ast
Full functional rescue of a co ...... vector-directed gene therapy.
@en
P2093
P2860
P1433
P1476
Full functional rescue of a co ...... vector-directed gene therapy.
@en
P2093
P2860
P304
P356
10.1128/JVI.74.3.1436-1442.2000
P577
2000-02-01T00:00:00Z