Advancements in gene transfer-based therapy for hemophilia A.
about
Enhanced biosynthesis of coagulation factor VIII through diminished engagement of the unfolded protein response.Generation of an optimized lentiviral vector encoding a high-expression factor VIII transgene for gene therapy of hemophilia AComparison of human coagulation factor VIII expression directed by cytomegalovirus and mammary gland-specific promoters in HC11 cells and transgenic miceDelivery of nucleic acid therapeutics by genetically engineered hematopoietic stem cells.State of the art: gene therapy of haemophilia.Engineered Hematopoietic Stem Cells as Therapeutics for Hemophilia A.A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice.Transplantation of retrovirally transduced bone marrow prevents autoimmune disease in aged mice by peripheral tolerance mechanisms.Factor VIII delivered by haematopoietic stem cell-derived B cells corrects the phenotype of haemophilia A mice.
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P2860
Advancements in gene transfer-based therapy for hemophilia A.
description
2009 nî lūn-bûn
@nan
2009 թուականի Դեկտեմբերին հրատարակուած գիտական յօդուած
@hyw
2009 թվականի դեկտեմբերին հրատարակված գիտական հոդված
@hy
2009年の論文
@ja
2009年論文
@yue
2009年論文
@zh-hant
2009年論文
@zh-hk
2009年論文
@zh-mo
2009年論文
@zh-tw
2009年论文
@wuu
name
Advancements in gene transfer-based therapy for hemophilia A.
@ast
Advancements in gene transfer-based therapy for hemophilia A.
@en
type
label
Advancements in gene transfer-based therapy for hemophilia A.
@ast
Advancements in gene transfer-based therapy for hemophilia A.
@en
prefLabel
Advancements in gene transfer-based therapy for hemophilia A.
@ast
Advancements in gene transfer-based therapy for hemophilia A.
@en
P2860
P356
P1476
Advancements in gene transfer-based therapy for hemophilia A.
@en
P2093
Christopher B Doering
H Trent Spencer
P2860
P304
P356
10.1586/EHM.09.63
P577
2009-12-01T00:00:00Z