Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides.
about
Inhibition of HIV-1 multiplication by antisense U7 snRNAs and siRNAs targeting cyclophilin AmiR-31 modulates dystrophin expression: new implications for Duchenne muscular dystrophy therapyEnhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapyCorrection of ClC-1 splicing eliminates chloride channelopathy and myotonia in mouse models of myotonic dystrophyGene therapy in clinical medicineAntisense-mediated exon skipping: a versatile tool with therapeutic and research applicationsAnimal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapyTargeted skipping of human dystrophin exons in transgenic mouse model systemically for antisense drug developmentInvestigating Synthetic Oligonucleotide Targeting of Mir31 in Duchenne Muscular DystrophyTherapeutic Potential of Tricyclo-DNA antisense oligonucleotidesNovel long noncoding RNAs (lncRNAs) in myogenesis: a miR-31 overlapping lncRNA transcript controls myoblast differentiationEfficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method.Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping.Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice.Genetic correction of splice site mutation in purified and enriched myoblasts isolated from mdx5cv mice.Guanine analogues enhance antisense oligonucleotide-induced exon skipping in dystrophin gene in vitro and in vivo.Long-term improvement in mdx cardiomyopathy after therapy with peptide-conjugated morpholino oligomers.Octa-guanidine morpholino restores dystrophin expression in cardiac and skeletal muscles and ameliorates pathology in dystrophic mdx mice.Gene and cell-mediated therapies for muscular dystrophy.Immunocytochemical analysis of human muscular dystrophy.Selective modification of alternative splicing by indole derivatives that target serine-arginine-rich protein splicing factors.A renaissance for antisense oligonucleotide drugs in neurology: exon skipping breaks new groundChimeric snRNA molecules carrying antisense sequences against the splice junctions of exon 51 of the dystrophin pre-mRNA induce exon skipping and restoration of a dystrophin synthesis in Delta 48-50 DMD cellsGene therapy for muscular dystrophies: progress and challengesExon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko miceNovel approaches to treat muscular dystrophies.Therapeutic exon skipping for dysferlinopathies?In-frame dystrophin following exon 51-skipping improves muscle pathology and function in the exon 52-deficient mdx mouse.The status of exon skipping as a therapeutic approach to duchenne muscular dystrophyBody-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model.One-year treatment of morpholino antisense oligomer improves skeletal and cardiac muscle functions in dystrophic mdx mice.High throughput screening in duchenne muscular dystrophy: from drug discovery to functional genomicsHuman Splicing Finder: an online bioinformatics tool to predict splicing signals.Therapeutic approaches to muscular dystrophy.Restoring dystrophin expression in duchenne muscular dystrophy muscle progress in exon skipping and stop codon read through.Small regulatory RNAs in mammals.MRI roadmap-guided transendocardial delivery of exon-skipping recombinant adeno-associated virus restores dystrophin expression in a canine model of Duchenne muscular dystrophy.Extensive and prolonged restoration of dystrophin expression with vivo-morpholino-mediated multiple exon skipping in dystrophic dogs.Splicing regulators: targets and drugsEffective rescue of dystrophin improves cardiac function in dystrophin-deficient mice by a modified morpholino oligomer.
P2860
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P2860
Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides.
description
1998 nî lūn-bûn
@nan
1998 թուականի Յուլիսին հրատարակուած գիտական յօդուած
@hyw
1998 թվականի հուլիսին հրատարակված գիտական հոդված
@hy
1998年の論文
@ja
1998年論文
@yue
1998年論文
@zh-hant
1998年論文
@zh-hk
1998年論文
@zh-mo
1998年論文
@zh-tw
1998年论文
@wuu
name
Modification of splicing in th ...... ntisense oligoribonucleotides.
@ast
Modification of splicing in th ...... ntisense oligoribonucleotides.
@en
Modification of splicing in th ...... ntisense oligoribonucleotides.
@nl
type
label
Modification of splicing in th ...... ntisense oligoribonucleotides.
@ast
Modification of splicing in th ...... ntisense oligoribonucleotides.
@en
Modification of splicing in th ...... ntisense oligoribonucleotides.
@nl
prefLabel
Modification of splicing in th ...... ntisense oligoribonucleotides.
@ast
Modification of splicing in th ...... ntisense oligoribonucleotides.
@en
Modification of splicing in th ...... ntisense oligoribonucleotides.
@nl
P2093
P356
P1476
Modification of splicing in th ...... ntisense oligoribonucleotides.
@en
P2093
Dunckley MG
Manoharan M
P304
P356
10.1093/HMG/7.7.1083
P577
1998-07-01T00:00:00Z