Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle
about
Targeted approaches to induce immune tolerance for Pompe disease therapyThe pharmacological chaperone AT2220 increases recombinant human acid α-glucosidase uptake and glycogen reduction in a mouse model of Pompe disease.Enzyme replacement therapy in late-onset Pompe disease: a systematic literature review.Preclinical Development of New Therapy for Glycogen Storage Diseases.β2 Agonists enhance the efficacy of simultaneous enzyme replacement therapy in murine Pompe disease.Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β2-Agonist in Murine Pompe Disease.Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.A beta-blocker, propranolol, decreases the efficacy from enzyme replacement therapy in Pompe disease.The Changing Face of Infantile Pompe Disease: A Report of Five Patients from the UAESalmeterol enhances the cardiac response to gene therapy in Pompe disease.Adjunctive β2-agonist treatment reduces glycogen independently of receptor-mediated acid α-glucosidase uptake in the limb muscles of mice with Pompe disease.Lysosomal storage diseases--the horizon expands.Glyco-engineering strategies for the development of therapeutic enzymes with improved efficacy for the treatment of lysosomal storage diseases.Pompe Disease: Diagnosis and Management. Evidence-Based Guidelines from a Canadian Expert Panel.The role of immune tolerance induction in restoration of the efficacy of ERT in Pompe disease.A Neuron-Specific Gene Therapy Relieves Motor Deficits in Pompe Disease Mice.Enhanced delivery of α-glucosidase for Pompe disease by ICAM-1-targeted nanocarriers: comparative performance of a strategy for three distinct lysosomal storage disorders.The new era of Pompe disease: advances in the detection, understanding of the phenotypic spectrum, pathophysiology, and management.Lysosomal Targeting Enhancement by Conjugation of Glycopeptides Containing Mannose-6-phosphate Glycans Derived from Glyco-engineered Yeast.
P2860
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P2860
Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle
description
2011 nî lūn-bûn
@nan
2011 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2011 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2011年の論文
@ja
2011年論文
@yue
2011年論文
@zh-hant
2011年論文
@zh-hk
2011年論文
@zh-mo
2011年論文
@zh-tw
2011年论文
@wuu
name
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@ast
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@en
type
label
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@ast
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@en
prefLabel
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@ast
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@en
P2093
P2860
P1476
Enhanced efficacy of enzyme re ...... expression in skeletal muscle
@en
P2093
Alison McVie-Wylie
Baodong Sun
Deeksha S Bali
Dwight D Koeberl
Songtao Li
Suhrad G Banugaria
Xiaoyan Luo
P2860
P304
P356
10.1016/J.YMGME.2011.02.006
P577
2011-02-13T00:00:00Z