Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
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Therapeutic approaches for shankopathiesComparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe micePreclinical Development of New Therapy for Glycogen Storage Diseases.Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β2-Agonist in Murine Pompe Disease.A beta-blocker, propranolol, decreases the efficacy from enzyme replacement therapy in Pompe disease.Salmeterol enhances the cardiac response to gene therapy in Pompe disease.Adjunctive β2-agonist treatment reduces glycogen independently of receptor-mediated acid α-glucosidase uptake in the limb muscles of mice with Pompe disease.Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction.Preclinical toxicology and biodistribution studies of recombinant adeno-associated virus 1 human acid α-glucosidase.Lysosomal storage diseases--the horizon expands.Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.Treatment Opportunities in Patients With Metabolic Myopathies.Immunomodulatory, liver depot gene therapy for Pompe disease.
P2860
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P2860
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
description
2012 nî lūn-bûn
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2012年の論文
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2012年学术文章
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2012年学术文章
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2012年学术文章
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2012年学术文章
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2012年学术文章
@zh-sg
2012年學術文章
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2012年學術文章
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2012年學術文章
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name
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@ast
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@en
type
label
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@ast
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@en
prefLabel
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@ast
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@en
P2093
P2860
P356
P1433
P1476
Adjunctive β2-agonists reverse neuromuscular involvement in murine Pompe disease.
@en
P2093
Andrew Bird
Baodong Sun
Beth L Thurberg
Deeksha Bali
Dwight D Koeberl
Mark A Tarnopolsky
Mats I Nilsson
Songtao Li
P2860
P356
10.1096/FJ.12-207472
P407
P577
2012-09-19T00:00:00Z