Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia.
about
Current and future alternative therapies for beta-thalassemia majorTowards in vivo amplification: Overcoming hurdles in the use of hematopoietic stem cells in transplantation and gene therapyProgresses towards safe and efficient gene therapy vectorsLentiviral mediated transgenesis by in vivo manipulation of spermatogonial stem cells.Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease.Lentivector integration sites in ependymal cells from a model of metachromatic leukodystrophy: non-B DNA as a new factor influencing integration.Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion.A method to sequence and quantify DNA integration for monitoring outcome in gene therapy.Long-term in vivo monitoring of mouse and human hematopoietic stem cell engraftment with a human positron emission tomography reporter gene.Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.Sites of retroviral DNA integration: From basic research to clinical applicationsProlonged Integration Site Selection of a Lentiviral Vector in the Genome of Human Keratinocytes.Development of gene therapy for thalassemia.Lentiviral vectors in cancer immunotherapy.Modeling correction of severe urea cycle defects in the growing murine liver using a hybrid recombinant adeno-associated virus/piggyBac transposase gene delivery system.Lack of genotoxicity due to foamy virus vector integration in human iPSCs.A microfluidics cytometer for mice anemia detection.Safe and Efficient Gene Therapy for Pyruvate Kinase DeficiencyCEP290 gene transfer rescues Leber congenital amaurosis cellular phenotype.Challenges in vector and trial design using retroviral vectors for long-term gene correction in hematopoietic stem cell gene therapy.Hepatic gene therapy using lentiviral vectors: has safety been established?Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient.Combining gene therapy and fetal hemoglobin induction for treatment of β-thalassemia.
P2860
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P2860
Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia.
description
2011 nî lūn-bûn
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2011 թուականի Մարտին հրատարակուած գիտական յօդուած
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2011 թվականի մարտին հրատարակված գիտական հոդված
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2011年の論文
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2011年学术文章
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2011年学术文章
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2011年学术文章
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2011年学术文章
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2011年学术文章
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2011年學術文章
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name
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@ast
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@en
type
label
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@ast
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@en
prefLabel
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@ast
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@en
P2093
P2860
P50
P356
P1433
P1476
Distribution of lentiviral vec ...... ansfer to treat β-thalassemia.
@en
P2093
Beatrix Gillet-Legrand
Charlotte Colomb
Floriane Fusil
Julian D Down
Kathleen Hehir
Keshet Ronen
Maria Denaro
Nirav Malani
Olivier Negre
Shannah Roth
P2860
P304
P356
10.1038/MT.2011.20
P577
2011-03-08T00:00:00Z