Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease.
about
Targeted approaches to induce immune tolerance for Pompe disease therapyImmune responses and hypercoagulation in ERT for Pompe disease are mutation and rhGAA dose dependent.Outcome of patients with classical infantile pompe disease receiving enzyme replacement therapy in Germany.Comparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe miceCRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapyOral delivery of Acid Alpha Glucosidase epitopes expressed in plant chloroplasts suppresses antibody formation in treatment of Pompe mice.Uricase alkaline enzymosomes with enhanced stabilities and anti-hyperuricemia effects induced by favorable microenvironmental changes.Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center studyLentiviral hematopoietic stem cell gene therapy in inherited metabolic disorders.Sustained immune tolerance induction in enzyme replacement therapy-treated CRIM-negative patients with infantile Pompe disease.Human-Induced Pluripotent Stem Cell-Based Modeling of Cardiac Storage Disorders.Immunological considerations for treating globoid cell leukodystrophy.European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience.Genetics of paediatric cardiomyopathies.High dose IVIG successfully reduces high rhGAA IgG antibody titers in a CRIM-negative infantile Pompe disease patient.Direct Intracranial Injection of AAVrh8 Encoding Monkey β-N-Acetylhexosaminidase Causes Neurotoxicity in the Primate Brain.Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.Current and Future Treatments for Lysosomal Storage Disorders.Enzyme replacement therapy for infantile-onset Pompe disease.Cardiac response to enzyme replacement therapy in infantile Pompe disease with severe hypertrophic cardiomyopathy.Pompe disease in adulthood: effects of antibody formation on enzyme replacement therapy.Long term clinical history of an Italian cohort of infantile onset Pompe disease treated with enzyme replacement therapy.
P2860
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P2860
Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease.
description
2014 nî lūn-bûn
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2014 թուականի Ապրիլին հրատարակուած գիտական յօդուած
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2014 թվականի ապրիլին հրատարակված գիտական հոդված
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2014年の論文
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年學術文章
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name
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@ast
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@en
type
label
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@ast
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@en
prefLabel
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@ast
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@en
P2093
P2860
P1476
Enzyme therapy and immune resp ...... assic infantile Pompe disease.
@en
P2093
Ans T van der Ploeg
Arnold J J Reuser
Carin M van Gelder
Marian A Kroos
Marianne Hoogeveen-Westerveld
P2860
P2888
P304
P356
10.1007/S10545-014-9707-6
P577
2014-04-09T00:00:00Z