CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
about
Durable and sustained immune tolerance to ERT in Pompe disease with entrenched immune responsesEvaluation of impact of anti-idursulfase antibodies during long-term idursulfase enzyme replacement therapy in mucopolysaccharidosis II patients.Sustained immune tolerance induction in enzyme replacement therapy-treated CRIM-negative patients with infantile Pompe disease.A pilot study on using rapamycin-carrying synthetic vaccine particles (SVP) in conjunction with enzyme replacement therapy to induce immune tolerance in Pompe disease.Long-term, high-level hepatic secretion of acid α-glucosidase for Pompe disease achieved in non-human primates using helper-dependent adenovirus.Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.A Humoral Immune Response Alters the Distribution of Enzyme Replacement Therapy in Murine Mucopolysaccharidosis Type I.Enzyme replacement therapy for infantile-onset Pompe disease.Enzyme replacement therapy with alglucosidase alfa in Pompe disease: Clinical experience with rate escalation.Response to de Vries et al.Improving the efficacy and safety of biologic drugs with tolerogenic nanoparticles.
P2860
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P2860
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@ast
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@en
type
label
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@ast
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@en
prefLabel
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@ast
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@en
P2093
P2860
P50
P356
P6366
P1433
P1476
CRIM-negative infantile Pompe ...... s treated with ERT monotherapy
@en
P2093
Amy S Rosenberg
Carolyn Ellaway
Deeksha S Bali
Eleanor G Botha
Jennifer Goldstein
Kaustuv Bhattacharya
Mihaela C Stefanescu
Nesrin Karabul
Priya S Kishnani
Sean N Prater
P2860
P2888
P304
P356
10.1038/GIM.2015.6
P407
P577
2015-03-05T00:00:00Z
P6366
2055737319