Neural stem cell gene therapy ameliorates pathology and function in a mouse model of globoid cell leukodystrophy.
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Moving towards effective therapeutic strategies for Neuronal Ceroid LipofuscinosisCombined gene/cell therapies provide long-term and pervasive rescue of multiple pathological symptoms in a murine model of globoid cell leukodystrophy.Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophyThe stem cell secretome and its role in brain repair.Experimental therapies in the murine model of globoid cell leukodystrophy.Gene therapy for lysosomal storage disorders: a good start.Effect of vitamin D3 intake on the onset of disease in a murine model of human Krabbe disease.Dynamic Activity of miR-125b and miR-93 during Murine Neural Stem Cell Differentiation In Vitro and in the Subventricular Zone Neurogenic Niche.Transplantation of mouse embryonic stem cell-derived oligodendrocytes in the murine model of globoid cell leukodystrophy.Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophyExtended normal life after AAVrh10-mediated gene therapy in the mouse model of Krabbe disease.Long-term Improvements in Lifespan and Pathology in CNS and PNS After BMT Plus One Intravenous Injection of AAVrh10-GALC in Twitcher MiceTransplantation of CD15-enriched murine neural stem cells increases total engraftment and shifts differentiation toward the oligodendrocyte lineageMissense mutation in mouse GALC mimics human gene defect and offers new insights into Krabbe diseaseWnt3a reestablishes osteogenic capacity to bone grafts from aged animals.Cellular transplant therapies for globoid cell leukodystrophy: Preclinical and clinical observationsPervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapyGlial progenitor cell-based treatment of the childhood leukodystrophies.MicroRNAs and Molecular Mechanisms of Neurodegeneration.Stem Cell Therapy for the Central Nervous System in Lysosomal Storage Diseases.Myelin repair by transplantation of myelin-forming cells in globoid cell leukodystrophy.Krabbe disease: One Hundred years from the bedside to the bench to the bedside.Perspective on innovative therapies for globoid cell leukodystrophy.Using magnetic nanoparticles for gene transfer to neural stem cells: stem cell propagation method influences outcomesRegion- and age-dependent alterations of glial-neuronal metabolic interactions correlate with CNS pathology in a mouse model of globoid cell leukodystrophy.Emerging stem cell therapies: treatment, safety, and biology.Two factor-based reprogramming of rodent and human fibroblasts into Schwann cells.Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy.A WNT protein therapeutic improves the bone-forming capacity of autografts from aged animals.Development of Multifunctional Magnetic Nanoparticles for Genetic Engineering and Tracking of Neural Stem Cells.Neural stem cells, a step closer to clinic?Human iPSC-based models highlight defective glial and neuronal differentiation from neural progenitor cells in metachromatic leukodystrophy.
P2860
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P2860
Neural stem cell gene therapy ameliorates pathology and function in a mouse model of globoid cell leukodystrophy.
description
2011 nî lūn-bûn
@nan
2011年の論文
@ja
2011年論文
@yue
2011年論文
@zh-hant
2011年論文
@zh-hk
2011年論文
@zh-mo
2011年論文
@zh-tw
2011年论文
@wuu
2011年论文
@zh
2011年论文
@zh-cn
name
Neural stem cell gene therapy ...... f globoid cell leukodystrophy.
@ast
Neural stem cell gene therapy ...... f globoid cell leukodystrophy.
@en
type
label
Neural stem cell gene therapy ...... f globoid cell leukodystrophy.
@ast
Neural stem cell gene therapy ...... f globoid cell leukodystrophy.
@en
prefLabel
Neural stem cell gene therapy ...... f globoid cell leukodystrophy.
@ast
Neural stem cell gene therapy ...... f globoid cell leukodystrophy.
@en
P2093
P2860
P50
P356
P1433
P1476
Neural stem cell gene therapy ...... of globoid cell leukodystrophy
@en
P2093
Aldo Orlacchio
Beatriz Alcala'-Franco
Chiara Cavazzin
Ilaria di Girolamo
Margherita Neri
P2860
P304
P356
10.1002/STEM.701
P577
2011-10-01T00:00:00Z