Single-dose intracerebroventricular administration of galactocerebrosidase improves survival in a mouse model of globoid cell leukodystrophy - Wikidata - wikimedia - TriplyDB

Single-dose intracerebroventricular administration of galactocerebrosidase improves survival in a mouse model of globoid cell leukodystrophy

Single-dose intracerebroventricular administration of galactocerebrosidase improves survival in a mouse model of globoid cell leukodystrophy

http://www.wikidata.org/entity/Q28296107

about

Lysosomal Re-acidification Prevents Lysosphingolipid-Induced Lysosomal Impairment and Cellular Toxicity Combined gene/cell therapies provide long-term and pervasive rescue of multiple pathological symptoms in a murine model of globoid cell leukodystrophy.Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy Experimental therapies in the murine model of globoid cell leukodystrophy.Gene therapy for lysosomal storage disorders: a good start.Glycosaminoglycan storage in neuroanatomical regions of mucopolysaccharidosis I dogs following intrathecal recombinant human iduronidase.Large-volume intrathecal enzyme delivery increases survival of a mouse model of late infantile neuronal ceroid lipofuscinosis.Neural stem cell gene therapy ameliorates pathology and function in a mouse model of globoid cell leukodystrophy.The myelin mutants as models to study myelin repair in the leukodystrophies.Specific antibody titer alters the effectiveness of intrathecal enzyme replacement therapy in canine mucopolysaccharidosis I.Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy Long-term Improvements in Lifespan and Pathology in CNS and PNS After BMT Plus One Intravenous Injection of AAVrh10-GALC in Twitcher Mice Fetal Brain-directed AAV Gene Therapy Results in Rapid, Robust, and Persistent Transduction of Mouse Choroid Plexus Epithelia Multipotent stromal cells alleviate inflammation, neuropathology, and symptoms associated with globoid cell leukodystrophy in the twitcher mouse.Continual Low-Dose Infusion of Sulfamidase Is Superior to Intermittent High-Dose Delivery in Ameliorating Neuropathology in the MPS IIIA Mouse Brain Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients.Insulin-like growth factor II peptide fusion enables uptake and lysosomal delivery of α-N-acetylglucosaminidase to mucopolysaccharidosis type IIIB fibroblasts.Myelin lesions associated with lysosomal and peroxisomal disorders.Emerging therapies for neurodegenerative lysosomal storage disorders - from concept to reality.Advances and pitfalls of cell therapy in metabolic leukodystrophies.Clinical Improvement of Alpha-mannosidosis Cat Following a Single Cisterna Magna Infusion of AAV1.Lithium improves cell viability in psychosine-treated MO3.13 human oligodendrocyte cell line via autophagy activation.Krabbe disease: One Hundred years from the bedside to the bench to the bedside.Treatment for Krabbe's disease: Finding the combination.Chaperones as potential therapeutics for Krabbe disease.Perspective on innovative therapies for globoid cell leukodystrophy.Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.Intracisternal enzyme replacement therapy in lysosomal storage diseases: dispersal pathways, regional enzyme concentrations and the effect of posttreatment posture.Evaluation of enzyme dose and dose-frequency in ameliorating substrate accumulation in MPS IIIA Huntaway dog brain.Delivering drugs to the central nervous system: an overview.Chaperone therapy for Krabbe disease: potential for late-onset GALC mutations.

P2860

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P2860

Single-dose intracerebroventricular administration of galactocerebrosidase improves survival in a mouse model of globoid cell leukodystrophy

http://www.wikidata.org/entity/Q28296107

description

2007 nî lūn-bûn

@nan

2007 թուականի Օգոստոսին հրատարակուած գիտական յօդուած

@hyw

2007 թվականի օգոստոսին հրատարակված գիտական հոդված

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2007年の論文

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2007年論文

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2007年論文

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2007年論文

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2007年論文

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2007年論文

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2007年论文

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name

Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Single-dose intracerebroventri ...... of globoid cell leukodystrophy

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Chad A Dicky

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Christopher B Eckman

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Frederick J Troendle

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Michael W DeLucia

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Wing C Lee

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Zeshan Ahmed

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2520-7

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10.1096/FJ.06-6169COM

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10

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21

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Dennis W. Dickson

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