Nanoparticles that deliver triplex-forming peptide nucleic acid molecules correct F508del CFTR in airway epithelium
about
In Vivo Delivery Systems for Therapeutic Genome EditingYear in review 2015: Interstitial lung disease, pulmonary vascular disease, pulmonary function, sleep and ventilation, cystic fibrosis and paediatric lung diseaseGenome-editing Technologies for Gene and Cell TherapyBarriers to inhaled gene therapy of obstructive lung diseases: A reviewIn vivo correction of anaemia in β-thalassemic mice by γPNA-mediated gene editing with nanoparticle deliveryLumacaftor and ivacaftor in the management of patients with cystic fibrosis: current evidence and future prospects.Cystic fibrosis lung environment and Pseudomonas aeruginosa infection.Improved i.p. drug delivery with bioadhesive nanoparticles.Gene-targeting pharmaceuticals for single-gene disorders.Nanotechnology for delivery of peptide nucleic acids (PNAs)Genetic medicines for CF: Hype versus reality.Versatility of peptide nucleic acids (PNAs): role in chemical biology, drug discovery, and origins of life.Impact of gene editing on the study of cystic fibrosis.Overview of CRISPR-Cas9 Biology.Cas9/gRNA targeted excision of cystic fibrosis-causing deep-intronic splicing mutations restores normal splicing of CFTR mRNA.Roadmap for an early gene therapy for cystic fibrosis airway disease.The cystic fibrosis transmembrane conductance regulator controls biliary epithelial inflammation and permeability by regulating Src tyrosine kinase activity.[A new toolbox for genome editing].Transformative therapies for rare CFTR missense alleles.To cleave or not to cleave: therapeutic gene editing with and without programmable nucleases.Peptide Nucleic Acids as a Tool for Site-Specific Gene Editing.Therapeutic Peptide Nucleic Acids: Principles, Limitations, and Opportunities.In utero nanoparticle delivery for site-specific genome editing.
P2860
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P2860
Nanoparticles that deliver triplex-forming peptide nucleic acid molecules correct F508del CFTR in airway epithelium
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@ast
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@en
type
label
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@ast
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@en
prefLabel
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@ast
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@en
P2093
P2860
P50
P356
P1476
Nanoparticles that deliver tri ...... 8del CFTR in airway epithelium
@en
P2093
Anisha Gupta
Christina Caputo
John P Geibel
Kavitha Anandalingam
Lee Polikoff
Marie E Egan
Nicole Ali McNeer
Rachel J Fields
Raman Bahal
Sascha Kopic
P2860
P2888
P356
10.1038/NCOMMS7952
P407
P577
2015-04-27T00:00:00Z