IPLEX administration improves motor neuron survival and ameliorates motor functions in a severe mouse model of spinal muscular atrophy.
about
Spinal muscular atrophy: from gene discovery to clinical trialsAssays for the identification and prioritization of drug candidates for spinal muscular atrophySystemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy.SMA-MAP: a plasma protein panel for spinal muscular atrophyMotor neuron cell-nonautonomous rescue of spinal muscular atrophy phenotypes in mild and severe transgenic mouse modelsSystemic administration of a recombinant AAV1 vector encoding IGF-1 improves disease manifestations in SMA miceAntisense-based therapy for the treatment of spinal muscular atrophySpinal muscular atrophy: an update on therapeutic progressMore than a bystander: the contributions of intrinsic skeletal muscle defects in motor neuron diseases.Developing therapies for spinal muscular atrophy.Polyethylene glycol-coupled IGF1 delays motor function defects in a mouse model of spinal muscular atrophy with respiratory distress type 1.Pharmacologically induced mouse model of adult spinal muscular atrophy to evaluate effectiveness of therapeutics after disease onset.A Perturbed MicroRNA Expression Pattern Characterizes Embryonic Neural Stem Cells Derived from a Severe Mouse Model of Spinal Muscular Atrophy (SMA).
P2860
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P2860
IPLEX administration improves motor neuron survival and ameliorates motor functions in a severe mouse model of spinal muscular atrophy.
description
2012 nî lūn-bûn
@nan
2012年の論文
@ja
2012年学术文章
@wuu
2012年学术文章
@zh-cn
2012年学术文章
@zh-hans
2012年学术文章
@zh-my
2012年学术文章
@zh-sg
2012年學術文章
@yue
2012年學術文章
@zh
2012年學術文章
@zh-hant
name
IPLEX administration improves ...... el of spinal muscular atrophy.
@ast
IPLEX administration improves ...... el of spinal muscular atrophy.
@en
type
label
IPLEX administration improves ...... el of spinal muscular atrophy.
@ast
IPLEX administration improves ...... el of spinal muscular atrophy.
@en
prefLabel
IPLEX administration improves ...... el of spinal muscular atrophy.
@ast
IPLEX administration improves ...... el of spinal muscular atrophy.
@en
P2093
P2860
P1433
P1476
IPLEX administration improves ...... el of spinal muscular atrophy.
@en
P2093
Andrea Luchetti
Antonio Filareto
Antonio Musarò
Arianna Malgieri
Elvira de Leonibus
Federica Sangiuolo
Gabriella Dobrowolny
Giuseppe Novelli
Luciano Saieva
Maria Chiara Quitadamo
P2860
P2888
P304
P356
10.2119/MOLMED.2012.00056
P407
P577
2012-09-25T00:00:00Z
P5875
P6179
1068965520