Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
about
Antisense oligonucleotide induction of progerin in human myogenic cellsDeletion of Dystrophin In-Frame Exon 5 Leads to a Severe Phenotype: Guidance for Exon Skipping Strategies.Learning And Improvement In Hereditary Diseases: Altnagelvin Hospital, Londonderry, 3rd December 2015.Targeted exon skipping to correct exon duplications in the dystrophin gene.Human RNAi pathway: crosstalk with organelles and cells.New developments in the use of gene therapy to treat Duchenne muscular dystrophy.Synthesis of a Morpholino Nucleic Acid (MNA)-Uridine Phosphoramidite, and Exon Skipping Using MNA/2'-O-Methyl Mixmer Antisense Oligonucleotide.Functional correction of dystrophin actin binding domain mutations by genome editing.A platform for discovery of functional cell-penetrating peptides for efficient multi-cargo intracellular delivery
P2860
Q35180565-863BC56B-B02F-4974-A646-5C02DE40208DQ35888871-051A1798-BEFD-44E7-9634-8E23AE858011Q37036835-10841907-5F53-414F-A649-68FCEED666DEQ37695543-98E2BAF9-DBBF-4912-BF92-3E968A02206DQ38160374-B4E11491-BCA7-4D90-9260-1A82AA010D4CQ38168863-1BD6C318-3973-44A1-A572-2448CB4D8316Q39159171-B6C6FC85-630F-4437-946A-097E44CAAC75Q42162721-74B1E30F-EA2D-47EA-9DDC-9B7F5334E9BCQ57524985-29964015-7440-474B-86FA-509B632C8C27
P2860
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
description
2012 nî lūn-bûn
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name
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
@ast
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
@en
type
label
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
@ast
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
@en
prefLabel
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
@ast
Targeted exon skipping to address "leaky" mutations in the dystrophin gene.
@en
P2093
P2860
P356
P1476
Targeted exon skipping to address "leaky" mutations in the dystrophin gene
@en
P2093
Brenda Wong
Carl F Adkin
Clayton Fragall
Francesco Muntoni
Kane Greer
Penny Meloni
Russell Johnsen
Steve D Wilton
P2860
P356
10.1038/MTNA.2012.40
P577
2012-10-16T00:00:00Z