Pharmacological small molecules for the treatment of lysosomal storage disorders.

Pharmacological small molecules for the treatment of lysosomal storage disorders.

Item
http://www.wikidata.org/entity/Q37799818
Novel patient cell-based HTS assay for identification of small molecules for a lysosomal storage diseaseA high throughput glucocerebrosidase assay using the natural substrate glucosylceramideDiscovery of a novel noniminosugar acid α glucosidase chaperone series.Biomarkers in the diagnosis of lysosomal storage disorders: proteins, lipids, and inhibodies.A phenotypic compound screening assay for lysosomal storage diseases.Glycolate Oxidase Is a Safe and Efficient Target for Substrate Reduction Therapy in a Mouse Model of Primary Hyperoxaluria Type IEnzymatic Screening and Diagnosis of Lysosomal Storage DiseasesStrategies for delivery of therapeutics into the central nervous system for treatment of lysosomal storage disorders.Targeting Wolman Disease and Cholesteryl Ester Storage Disease: Disease Pathogenesis and Therapeutic Development.Pharmacological chaperone therapy for Gaucher disease: a patent review.Bicyclic derivatives of L-idonojirimycin as pharmacological chaperones for neuronopathic forms of Gaucher disease.A systematic investigation of iminosugar click clusters as pharmacological chaperones for the treatment of Gaucher disease.Molecular therapy of primary hyperoxaluria.Targeted delivery of pharmacological chaperones for Gaucher disease to macrophages by a mannosylated cyclodextrin carrier.
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Pharmacological small molecules for the treatment of lysosomal storage disorders.

Item
http://www.wikidata.org/entity/Q37799818
description
article científic
@ca
article scientifique
@fr
articolo scientifico
@it
artigo científico
@pt
bilimsel makale
@tr
scientific article published on 13 October 2010
@en
vedecký článok
@sk
vetenskaplig artikel
@sv
videnskabelig artikel
@da
vědecký článek
@cs
name
Pharmacological small molecules for the treatment of lysosomal storage disorders.
@en
Pharmacological small molecules for the treatment of lysosomal storage disorders.
@nl
type
label
Pharmacological small molecules for the treatment of lysosomal storage disorders.
@en
Pharmacological small molecules for the treatment of lysosomal storage disorders.
@nl
prefLabel
Pharmacological small molecules for the treatment of lysosomal storage disorders.
@en
Pharmacological small molecules for the treatment of lysosomal storage disorders.
@nl
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P1476
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P2860
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P921
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Pharmacological small molecules for the treatment of lysosomal storage disorders
@en
P2093
P2860
P304
P31
P356
10.1517/13543784.2010.524205
P407
P433
P478
P50
P577
P698
P921