Potential therapeutic applications of antisense morpholino oligonucleotides in modulation of splicing in primary immunodeficiency diseases
about
Arginine-rich cell-penetrating peptide dramatically enhances AMO-mediated ATM aberrant splicing correction and enables delivery to brain and cerebellum.Functional characterization and targeted correction of ATM mutations identified in Japanese patients with ataxia-telangiectasia.Intronic polyadenylation of PDGFRα in resident stem cells attenuates muscle fibrosis.In vitro correction of a novel splicing alteration in the BTK gene by using antisense morpholino oligonucleotides.Tricyclanos: conformationally constrained nucleoside analogues with a new heterotricycle obtained from a d-ribofuranose unit.
P2860
Potential therapeutic applications of antisense morpholino oligonucleotides in modulation of splicing in primary immunodeficiency diseases
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 13 December 2010
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Potential therapeutic applicat ...... mary immunodeficiency diseases
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Potential therapeutic applicat ...... ary immunodeficiency diseases.
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type
label
Potential therapeutic applicat ...... mary immunodeficiency diseases
@en
Potential therapeutic applicat ...... ary immunodeficiency diseases.
@nl
prefLabel
Potential therapeutic applicat ...... mary immunodeficiency diseases
@en
Potential therapeutic applicat ...... ary immunodeficiency diseases.
@nl
P2860
P1476
Potential therapeutic applicat ...... mary immunodeficiency diseases
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P2093
Richard A Gatti
P2860
P356
10.1016/J.JIM.2010.12.001
P577
2010-12-13T00:00:00Z