Adeno-associated virus vectors and neurological gene therapy.
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Targeting adeno-associated virus and adenoviral gene therapy for hepatocellular carcinomaBiophysical Properties of Optogenetic Tools and Their Application for Vision Restoration ApproachesSystemic gene delivery to the central nervous system using Adeno-associated virus.Enhanced selective gene delivery to neural stem cells in vivo by an adeno-associated viral variantAnti-Epidermal Growth Factor Receptor Gene Therapy for GlioblastomaProspects for engineering neurons from local neocortical cell populations as cell-mediated therapy for neurological disordersGlucocorticoid Cell Priming Enhances Transfection Outcomes in Adult Human Mesenchymal Stem Cells.Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brainSystemic gene delivery transduces the enteric nervous system of guinea pigs and cynomolgus macaques.Distribution, physiology and pharmacology of relaxin-3/RXFP3 systems in brain.Preclinical study of rAAV2-sTRAIL: pharmaceutical efficacy, biodistribution and safety in animals.Gene therapy approaches in the non-human primate model of Parkinson's disease.Adeno-Associated Virus (AAV) as a Vector for Gene Therapy.AAV serotypes have distinctive interactions with domains of the cellular receptor AAVR.miRNA-mediated post-transcriptional silencing of transgenes leads to increased adeno-associated viral vector yield and targeting specificity.AAV-based dual-reporter circuit for monitoring cell signaling in living human cells.A Designer AAV Variant Permits Efficient Retrograde Access to Projection Neurons.CNS-restricted Transduction and CRISPR/Cas9-mediated Gene Deletion with an Engineered AAV Vector.Effects of AAV-mediated knockdown of nNOS and GPx-1 gene expression in rat hippocampus after traumatic brain injury.In Vivo Selection of a Computationally Designed SCHEMA AAV Library Yields a Novel Variant for Infection of Adult Neural Stem Cells in the SVZ.The human brain endothelial barrier: transcytosis of AAV9, transduction by AAV2: An Editorial Highlight for 'Trafficking of adeno-associated virus vectors across a model of the blood-brain barrier; a comparative study of transcytosis and transductioNovel GP64 envelope variants for improved delivery to human airway epithelial cells.Viral Cre-LoxP tools aid genome engineering in mammalian cells.Targeted in vivo genetic manipulation of the mouse or rat brain by in utero electroporation with a triple-electrode probe.Imaging of electrical activity in small diameter fibers of the murine peripheral nerve with virally-delivered GCaMP6f.Engineered viral vectors for functional interrogation, deconvolution, and manipulation of neural circuits.Recent progress and considerations for AAV gene therapies targeting the central nervous system.Translation of MicroRNA-Based Huntingtin-Lowering Therapies from Preclinical Studies to the Clinic.In vivo methods for acute modulation of gene expression in the central nervous system
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P2860
Adeno-associated virus vectors and neurological gene therapy.
description
article científic
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article scientifique
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articol științific
@ro
articolo scientifico
@it
artigo científico
@gl
artigo científico
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artigo científico
@pt-br
artikel ilmiah
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artikull shkencor
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artículo científico
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name
Adeno-associated virus vectors and neurological gene therapy.
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type
label
Adeno-associated virus vectors and neurological gene therapy.
@en
prefLabel
Adeno-associated virus vectors and neurological gene therapy.
@en
P2093
P2860
P356
P1433
P1476
Adeno-associated virus vectors and neurological gene therapy.
@en
P2093
David S Ojala
David V Schaffer
Dominic P Amara
P2860
P356
10.1177/1073858414521870
P577
2014-02-20T00:00:00Z